Orchard Therapeutics - U.S.

Dedicated to transforming the lives of patients with inherited diseases through innovative gene therapy.

[Orchard Therapeutics - U.S. @orchard_tx]

Today we recognize and celebrate #RareDiseaseDay with the more than 300 million people worldwide living with a rare disease. Learn more about how to get involved: https://t.co/wr16mLQz1b.

#RareDiseaseDay #ShowYourRare #EndTheDiagnosticOdyssey #SupportRareDiseases

[Orchard Therapeutics - U.S. @orchard_tx]

We commend @HHSGov leadership for recognizing the immense and urgent medical need to screen for #MLD at birth by adding the condition to the Recommended Uniform Screening Panel (RUSP).

Read more: https://t.co/Hkop65Ncle. #newbornscreening #raredisease

[Orchard Therapeutics - U.S. @orchard_tx]

Earlier this week, patients and families, advocates and clinicians gathered on Capitol Hill to educate legislators on the importance of newborn screening for metachromatic leukodystrophy (#MLD), a rapidly progressing, irreversible and ultimately fatal pediatric disease.

[Orchard Therapeutics - U.S. @orchard_tx]

Today is World Sanfilippo Awareness Day. Join us in spreading awareness about this rare and life-limiting neurometabolic disease. Visit @CureSanfilippoF for more information: https://t.co/ycgBNSOiAa #WorldSanfilippoDay

[Orchard Therapeutics - U.S. @orchard_tx]

Our team looks forward to connecting with colleagues and peers at #iciem2025! Click here for more information: https://t.co/nf5Np1iA8V.

[Orchard Therapeutics - U.S. @orchard_tx]

Our team looks forward to participating in #epns2025! Click here for more information: https://t.co/jL0K7H4yOS.

[Orchard Therapeutics - U.S. @orchard_tx]

At Orchard, diversity is key to our strength and vibrancy, which is why inclusion and allyship are not confined to one day, week or month. #OrchardProud

[Orchard Therapeutics - U.S. @orchard_tx]

Tomorrow is International Neonatal Screening Day. We stand with like-minded organizations dedicated to advancing #NewbornScreening for treatable genetic diseases. Learn more: https://t.co/wdxrrWA5Mz

[Orchard Therapeutics - U.S. @orchard_tx]

Today is #MPSAwarenessDay. We join with the community to shine a light on this group of rare, life-limiting, inherited genetic diseases. Learn more at: https://t.co/fM5vu44BAX.

[Orchard Therapeutics - U.S. @orchard_tx]

We are honored to recognize and celebrate #RareDiseaseDay with the more than 300 million people worldwide living with a rare disease. Learn more about how to get involved: https://t.co/Pom1Kd7mt4.

#RareDiseaseDay #ShowYourRare #EndTheDiagnosticOdyssey #SupportRareDiseases

[Orchard Therapeutics - U.S. @orchard_tx]

We are looking forward to participating at #ssiem2024! Learn more: https://t.co/q9wJsXMlyR

[Orchard Therapeutics - U.S. @orchard_tx]

We look forward to participating in the @RSTMH event “Unveiling Gene Therapy: Transforming medical practice through ATMPs.” Learn more: https://t.co/qZ9zGZHtQc.

[Orchard Therapeutics - U.S. @orchard_tx]

On International Neonatal Screening Day #INSD, learn more about the progress being made to advance newborn screening #NBS for metachromatic leukodystrophy #MLD: https://t.co/eQrUKjAq6G.

[Orchard Therapeutics - U.S. @orchard_tx]

We are excited to join the leukodystrophy community in taking strides to support @ELAOfficielle ‘Met tes baskets’ (wear your trainers) at work international challenge! Learn more at: https://t.co/tGdfiL2Yjz.

[Orchard Therapeutics - U.S. @orchard_tx]

Today is #MPSAwarenessDay. We join with the community to shine a light on this group of rare, life-limiting, inherited genetic diseases. Learn more at: https://t.co/vrvUUflFEj.

[Orchard Therapeutics - U.S. @orchard_tx]

We are incredibly proud our fearless leader, Dr. @bobby_gaspar, has been named to the inaugural 2024 #TIME100HEALTH list. Please read our press release for more information: https://t.co/drbF0gDS5k, and see the full list of honorees here: https://t.co/KiPNo00NvR.

[Orchard Therapeutics - U.S. @orchard_tx]

Today we outlined our U.S. launch plans for Lenmeldy™ (atidarsagene autotemcel), the only approved therapy for eligible children with early-onset metachromatic leukodystrophy. Read more: https://t.co/cLJPtG1gEn

[Orchard Therapeutics - U.S. @orchard_tx]

We are thrilled to announce that the @US_FDA has approved Lenmeldy™ (atidarsagene autotemcel), the only therapy for eligible children with early-onset metachromatic leukodystrophy in the U.S. Read more in our press release: https://t.co/loHlBb22V7.

[Orchard Therapeutics - U.S. @orchard_tx]

On #RareDiseaseDay please join us in helping raise awareness and #ShowYourColours in support of the millions of people living with rare diseases. Learn more at https://t.co/8jgyXnSXSi

[Orchard Therapeutics - U.S. @orchard_tx]

We look forward to participating in @WORLDSymposia 2024 and hosting a symposia featuring expert speakers sharing their knowledge and experience to establish new standards and advance #newbornscreening through interdisciplinary collaboration. Learn more: https://t.co/bR0aiKHJk3