PTC Therapeutics

PTC is a patient-centered biopharmaceutical company focused on discovering, developing & commercializing medicine for patients with rare disease

[PTC Therapeutics @PTCBio]

Hello, #FabryDisease community. We're honored to introduce ourselves as we advance the investigational gene therapy ST-920 with an FDA submission planned before the end of 2026. Read our letter to the community: https://t.co/nqXAh4ecTE

[PTC Therapeutics @PTCBio]

PTC will participate in three upcoming investor conferences in September. Learn more: https://t.co/pKULuQdz0q

[PTC Therapeutics @PTCBio]

#SSIEM2026 is a meaningful moment for the PKU community. At the meeting multiple scientific data presentations spanning research, clinical outcomes & real-world case studies will be featured. https://t.co/afJ5qCnDaC

[PTC Therapeutics @PTCBio]

PTC Therapeutics was selected as the winning bidder to acquire ST-920 – a BLA-stage one-time administered AAV gene therapy for Fabry disease – from Sangamo Therapeutics in a competitive bankruptcy auction. Learn more: https://t.co/wwWMnHlwam

[PTC Therapeutics @PTCBio]

PTC Therapeutics welcomes Hege Sollie-Zetlmayer to its Board of Directors. With 30 years experience in biopharma and medical devices, including eight at PTC as CHRO, she brings deep global leadership to advance our mission for patients with rare diseases.

[PTC Therapeutics @PTCBio]

Today we announced our Q2 2026 financial results, highlighting strong commercial momentum with accelerating global uptake of our treatment for PKU. Learn more in our press release: https://t.co/UyYhlTlfBZ | Webcast: https://t.co/UGR3VAvAvo

[PTC Therapeutics @PTCBio]

PTC will host a web conference to report our second quarter 2026 financial results and provide an update on the company’s business on Thursday, July 30, 2026, at 4:30 p.m. ET. Learn more: https://t.co/bHIcn2szJk

[PTC Therapeutics @PTCBio]

Every day, the #PKU community faces unseen challenges. This #InternationalPKUDay, PTC is making a #PledgeForPKU: to listen, learn and support everyone this journey. Join us in championing hope, access and a future without limits. https://t.co/T2bJ06R9zx

[PTC Therapeutics @PTCBio]

Ahead of International PKU Day, we’re spotlighting mental health in the PKU community. Kevin, Signe & Regina share their journeys with stigma, anxiety & resilience. Learn more about their stories: https://t.co/iHIMbpnIfb

[PTC Therapeutics @PTCBio]

Our 2025 Corporate Social Responsibility Report highlights a year of focus, execution and measurable progress delivering differentiated medicines for people with rare disorders. See how we're driving impact across access, innovation, people & our planet: https://t.co/e7DPQFYYr0

[PTC Therapeutics @PTCBio]

On #ClinicalTrialsDay, we honor patients, families, and clinical teams advancing rare disease research. This year's #ResearchRising theme reminds us that progress comes from partnership and trust. Learn more: https://t.co/bLGGMx68AS

[PTC Therapeutics @PTCBio]

May is Friedreich’s ataxia (FA) Awareness Month and we're proud to honor the strength of those living with this rare condition. Kailey’s journey reflects the challenges many face, from recognizing symptoms to finding support. Learn more: https://t.co/4chhhoTIaO

[PTC Therapeutics @PTCBio]

Some days, the hardest part of living with a rare disorder isn’t what others can see—it’s the uncertainty: navigating genetic testing barriers and painful life changes. During #HDAwarenessMonth, PTC is proud to share stories like April's. Learn more: https://t.co/AbAfY1YeUO

[PTC Therapeutics @PTCBio]

Today, we announced our Q1 2026 financial results, highlighting record performance and continued momentum across the business—led by the global launch of our treatment for #PKU. See the release: https://t.co/WZWGYhO9HI and webcast recording: https://t.co/rbUFTSbIOO

[PTC Therapeutics @PTCBio]

PTC will participate in three upcoming investor conferences in May and June. Learn more: https://t.co/zlkoMGdsDg

[PTC Therapeutics @PTCBio]

This #NationalPKUAwarenessMonth, we’re honoring the resilience of the PKU community. Living with PKU is more than a diet—it takes constant planning, advocacy and support. Amanda’s story, alongside her mom Jill, helps make the invisible visible. Learn more: https://t.co/HMuBv6cSOY

[PTC Therapeutics @PTCBio]

On Rare Disease Day, we recognize the millions living with rare conditions. At PTC, we know that progress starts with listening to those impacted. Together, we can make a difference. Learn more: https://t.co/WNnypjEt54

[PTC Therapeutics @PTCBio]

PTC will participate in three upcoming investor conferences in March, including TD Cowen 46th Annual Health Care Conference, Leerink 2026 Global Healthcare Conference and the Barclays Global Healthcare Conference. Learn more: https://t.co/oAgAxg3AAS

[PTC Therapeutics @PTCBio]

PKU is rare—but the PKU community’s strength is extraordinary. Living with PKU means daily planning, monitoring, and resilience. This Rare Disease Day, we’re amplifying their voices. Watch, listen, and share their stories: https://t.co/c6vmiMhNUV

[PTC Therapeutics @PTCBio]

Today, we announced our Q4 and full-year 2025 financial results, highlighting strong revenue performance that sets the stage for continued growth and innovation in the coming year. Learn more in our release: https://t.co/b8LbsRD7J9 and webcast recording: https://t.co/L9P8TI8zQG