After a ten-year misdiagnosis, Caffrey and his family have been navigating their #Duchenne journey for the past four years. We are grateful to have spent time with them to learn how they found their new normal and what gives them hope for the future.
RT @WaveLifeSci: We are excited to announce we have achieved the first-ever therapeutic #RNAediting in humans in our RestorAATion-2 trial oRT @WaveLifeSci: We are excited to announce we have achieved the first-ever therapeutic #RNAediting in humans in our RestorAATion-2 trial oRT @WaveLifeSci: We are excited to announce we have achieved the first-ever therapeutic #RNAediting in humans in our RestorAATion-2 trial oRT @WaveLifeSci: We are excited to announce we have achieved the first-ever therapeutic #RNAediting in humans in our RestorAATion-2 trial o…
We are pleased to announce positive interim data from the Phase 2 FORWARD-53 trial in #Duchenne. Join us this morning at 8:30 a.m. ET for an investor conference call where we’ll discuss the results. Link to call: https://t.co/EbpmtM6ZL3
This morning, we shared positive data from the Phase 2 FORWARD-53 study where we observed substantial dystrophin expression and a safe and well tolerated profile for WVE-N531 in #Duchenne. Learn more about these data and what’s next. $WVE
Today we announced positive results from the Phase 1b/2a SELECT-HD study with the first clinical demonstration of allele-selective mutant huntingtin lowering in #HuntingtonsDisease. $WVE
Great recognition for Wave as one of the top editing companies. Thank you @Alex Philippidis and @Genetic Engineering & Biotechnology News for highlighting our progress leading the clinical advancement of #RNAediting to transform the lives of patients.
.@FortuneMagazine & @GPTW_US recognized us as a #Fortune#BestWorkplaces for Women AND we're the highest ranked #Biotech company on the list! We enable our employees to achieve their full potential so we can deliver new medicines & help people live longer, healthier lives.
We believe in being a force for good. Our annual #CommunityService Week is one way we make an impact in our communities through our Helping Hands: Alnylam Volunteers program. This year, over 800 employees provided 2,000+ hours of service at 50 projects in the US, Europe & Asia.
We’re thrilled to share the news that we have received @US_FDA approval for AMVUTTRA (vutrisiran), the fifth #RNAi therapeutic developed by Alnyam to receive regulatory approval in less than four years. #raredisease#biotech#RNAitherapeutics#siRNA
@Jbrekkie Hey @Jbrekkie! Amazing set last night at @RoyaleBoston! New stuff sounded great & loved the @DollyParton cover! Since you're still in Boston, maybe you could BE SWEET to a local org like ours and help start a weekend Jubilee for our students! 🙂 https://t.co/SpCzSGdxyA
📅 Save the date! 📅
You're invited to Perkins' inaugural walk, "Everybody In! #MoveForPerkins" on Saturday, October 2. Join us to create a more inclusive, accessible world of opportunities for all people. #DisabilityTwitter https://t.co/QdHk2LrFP7