It is the time of the year when we review the #Dravet syndrome pipeline:
- 2 drugs approved
- 12 more candidates in development
- 11 orphan designations
- ASOs and gene therapy approaching trials
So much progress!!
Full pipeline review in my website: https://t.co/p4JCwL4tEK
We are a Private R&D Organisation further evolving the vision of a more collaborative and direct way of working with pharmaceutical industries, academia and funding agencies. Check out what we do in our latest animation and stay tuned for the launch of our website... coming soon!
Thank you @MarinusPharma for helping the #CDKL5 community have such fantastic videos! Running the first pivotal trial ever in CDD was already a major contribution, and helping us put together meetings like the @CDKL5Alliance one show you #CareAboutRare 💜
https://t.co/c2zgj5rldi