CureDuchenne

We are committed to improving the lives of those affected by Duchenne through accelerating research, improving care and empowering the community.

[CureDuchenne @CureDuchenne]

REGISTER: https://t.co/Pppt3D4rLG

#DMD #duchenne #exonskipping #CureDuchenne

[CureDuchenne @CureDuchenne]

Most boys with Duchenne don't live beyond their 20s.

Every candle is a reminder that time is precious—and that we need a cure.

Help us find the cure.

Visit https://t.co/akfcLWLQ80 💙

#CureDuchenne #Duchenne #DMD #ACureCantWait #RareDisease

[CureDuchenne @CureDuchenne]

Looking for what’s next in Duchenne research?

See our updated list of clinical trials, studies actively enrolling, and new therapies being tested.

Visit the full list: https://t.co/fNuYg7LYky

#Clinicaltrials #Science #Raredisease #DMD

[CureDuchenne @CureDuchenne]

In this video from Muscular Dystrophy News, Sheryl Marrazzo Community Engagement Coordinator at CureDuchenne shares how charting baseline measurements, medications, symptoms, and health trends has helped her advocate for her son's care.
🎥 https://t.co/serWv76VMK
#DMD

[CureDuchenne @CureDuchenne]

Today, we launch A Cure Can't Wait.
Duchenne doesn't wait. Neither can we. For families living with Duchenne, every birthday is both a celebration and a reminder of how valuable time is.
💙 https://t.co/E83KAYbQAA 💙
#CureDuchenne #Duchenne #DMD #ACureCantWait #RareDisease

[CureDuchenne @CureDuchenne]

https://t.co/OjywLwl7Td

[CureDuchenne @CureDuchenne]

CureDuchenne was an early funder of @Avidity Biosciences, which is now a @Novartis company.  They have submitted a BLA to the FDA for delpacibart zotadirsen (“del-zota”) as a treatment option for individuals with Duchenne amenable to skipping exon 44
https://t.co/brxVm1yQqb

[Dyne Therapeutics @Dyne_tx]

Today we welcomed Barry Greene to Dyne’s Board of Directors. Barry’s strong biopharmaceutical experience spanning nearly three decades will be valuable as we continue progressing toward potential commercialization.

Read more: https://t.co/RhYjPeTqv9

[CureDuchenne @CureDuchenne]

https://t.co/9zI5DIcZb9

[CureDuchenne @CureDuchenne]

As a founding partner and initial funder of the Collaborative Trajectory Analysis Project (cTAP), CureDuchenne is proud to support an important advancement

https://t.co/gcHBK82cPF

#DMD #Duchenne #CureDuchenne

[CureDuchenne @CureDuchenne]

The conversations from FUTURES 2026 don't have to end here. 💙

Many of our main presentations are now available on YouTube, featuring research updates, clinical insights, and community stories.

https://t.co/85vh8nt3CT

[CureDuchenne @CureDuchenne]

“This is really the Holy Grail, to be able to deliver the full-length dystrophin,” said Debra Miller, CEO of CureDuchenne, a nonprofit group that participated in SonoThera’s new financing through a subsidiary, CureDuchenne Ventures.
https://t.co/IhDlcoX2fI

[CureDuchenne @CureDuchenne]

We are pleased to announce a new investment in SonoThera, supporting the advancement of its targeted, ultrasound-mediated gene delivery technology focused on the delivery of full-length dystrophin.

https://t.co/TafyzHJDji

#SonoThera #CureDuchenne
#dmd #GeneTherapy

[CureDuchenne @CureDuchenne]

Every child deserves hope. 💙 Support CureDuchenne's mission to fund research, improve care, and accelerate treatments for Duchenne muscular dystrophy. Make your impact today: https://t.co/tqKrDyE3fF #CureDuchenne https://t.co/tqKrDyE3fF

[CureDuchenne @CureDuchenne]

#dmd #ADA #Duchenne #musculardystrophy

[CureDuchenne @CureDuchenne]

FUTURES 2027 is heading to San Diego! May 27–30 at the Marriott Marquis San Diego Marina.

Education, breakthroughs, connection, and yes... the legendary FUTURES Party!

Early bird rates are available now. Lock in your lowest price before they're gone.
https://t.co/3k77U3b9zI

[REGENXBIO @REGENXBIO]

We’re thrilled to join the Duchenne community in Orlando at @CureDuchenne FUTURES. Tomorrow our Executive Director of Medical Affairs, Koji Takahashi, will discuss our RGX-202 program including the recent, positive topline pivotal data. Looking forward to connecting! #FUTURES2026

[CureDuchenne @CureDuchenne]

@TevardB

https://t.co/YtPS4BpjME

[Dyne Therapeutics @Dyne_tx]

Today we announced initiation of the Phase 3 confirmatory FORZETTO trial evaluating z-rostudirsen in exon 51 DMD.

See the full press release here: https://t.co/AknVplJ3hR

[CureDuchenne @CureDuchenne]

Get ready for an unforgettable evening filled with glow-in-the-dark fun! Lets light up the night as we gather together for an evening of connection, celebration, and unforgettable memories.

Register today using the link below! https://t.co/NZopFelnXO

#DMD #Florida