Exciting publication for the @Phelan_McDermid community. Research out of Univ Buffalo this past week is shedding light on possible targets for new treatment development. Each paper like this, another important step forward!!! https://t.co/lK7lnQrrmA
Exciting news for the MPS/Sly syndrome community around the world, and to all my friends and colleagues at Ultragenyx - Great work and congrats! https://t.co/hHOfNwXhQq