Neonatal expression of human FMRP isoform rescues cortical processing deficits and improves behaviors in a mouse model of Fragile X Syndrome https://t.co/m9UKngzFGm #MTNA
Cerebrospinal Delivery of a Bidirectional Aav9 Vector Improves Optic Nerve and Retinal Pathology in a Sheep Model of Tay-Sachs Disease https://t.co/aL17fM01a5 #genetherapy#celltherapy
The thymidine analog azidothymidine potentiates the immunomodulatory function of interferon-α in adult T-cell leukemia/lymphoma https://t.co/mogY85yARo #genetherapy#celltherapy
Pyroptosis as a Novel Therapeutic Target in Glioblastoma Multiforme: Mechanisms, Molecular Insights and Therapeutic Potential https://t.co/vXI07x4503 #MTNA
Therapeutic potential of three-dimensional hepatocyte-like cells from human adipose-derived mesenchymal stem cells in urea cycle disorders. https://t.co/K0E2ow5qLK #genetherapy#celltherapy
Targeting emerging respiratory pathogens with Clamp Peptides: broad-spectrum inhibition of viral entry in 3D human lung models https://t.co/48QvLF0T4F #genetherapy#celltherapy
Antibody Format Matters: A Comparative Analysis of VHH and scFv Domains Reveals Superior In Vivo CAR T Cell Function with VHH Domains https://t.co/LjfiLRGo3u #genetherapy#celltherapy
Milk-Derived Extracellular Vesicles Loaded with miR-146a-5p as a Novel Therapeutic Strategy for Allergic Airway Inflammation https://t.co/78EvsfRcVK #MTNA