Molecular Therapy Family of Journals

The leading family of journals in cell and gene therapy. Journals include Molecular Therapy, Advances, Nucleic Acids, and Oncology.

[Molecular Therapy Family of Journals @MolTherapy]

Neonatal expression of human FMRP isoform rescues cortical processing deficits and improves behaviors in a mouse model of Fragile X Syndrome https://t.co/m9UKngzFGm #MTNA

[Molecular Therapy Family of Journals @MolTherapy]

Antimetabolites synergize with antibody drug conjugate-based non-genotoxic conditioning facilitating hematopoietic stem cell-directed lentiviral gene therapy https://t.co/mwh2WLusSN #MTMCD

[Molecular Therapy Family of Journals @MolTherapy]

Cerebrospinal Delivery of a Bidirectional Aav9 Vector Improves Optic Nerve and Retinal Pathology in a Sheep Model of Tay-Sachs Disease https://t.co/aL17fM01a5 #genetherapy #celltherapy

[Molecular Therapy Family of Journals @MolTherapy]

The thymidine analog azidothymidine potentiates the immunomodulatory function of interferon-α in adult T-cell leukemia/lymphoma https://t.co/mogY85yARo #genetherapy #celltherapy

[Molecular Therapy Family of Journals @MolTherapy]

Comparative evaluation of oncolytic viruses reveals opposing preferences for glioblastoma subtypes https://t.co/LnFNTETy6v

[Molecular Therapy Family of Journals @MolTherapy]

A novel combination approach targeting P300 and DNA-PK exploits epigenetic dependencies in acute myeloid leukemia https://t.co/ScSDj4Mn6V

[Molecular Therapy Family of Journals @MolTherapy]

CRISPR/Cas9 screening reveals TM9SF2 knockout as a solution to HEK293 cell aggregation for improved AAV production https://t.co/SBHDx0KTJv #MTMCD

[Molecular Therapy Family of Journals @MolTherapy]

Pyroptosis as a Novel Therapeutic Target in Glioblastoma Multiforme: Mechanisms, Molecular Insights and Therapeutic Potential https://t.co/vXI07x4503 #MTNA

[Molecular Therapy Family of Journals @MolTherapy]

FDA issues new draft guidance on human gene therapy products incorporating genome editing https://t.co/i3TjgBPjqU #genetherapy #celltherapy

[Molecular Therapy Family of Journals @MolTherapy]

In this issue https://t.co/MsMTOvaWWT #genetherapy #celltherapy

[Molecular Therapy Family of Journals @MolTherapy]

Therapeutic potential of three-dimensional hepatocyte-like cells from human adipose-derived mesenchymal stem cells in urea cycle disorders. https://t.co/K0E2ow5qLK #genetherapy #celltherapy

[Molecular Therapy Family of Journals @MolTherapy]

Next-generation LMP2A-targeting TCR-recombinant T cells with inducible IL-18 expression to treat EBV-associated malignancies https://t.co/12m8RPfscI

[Molecular Therapy Family of Journals @MolTherapy]

Oncolytic virus-delivered GSDME: Unlocking pyroptosis to improve dendritic cell function and amplify cytotoxic T cell response https://t.co/wh1VyFvNup

[Molecular Therapy Family of Journals @MolTherapy]

Intra-CNS AAV9-GBA1 delivery yields species and route of administration differences in safety and transgene expression https://t.co/eqFwzFgmQl #MTMCD

[Molecular Therapy Family of Journals @MolTherapy]

NK cell immunotherapy after analytic treatment interruption is associated with HIV viral control. https://t.co/KqK39jF3U7 #MTMCD

[Molecular Therapy Family of Journals @MolTherapy]

Targeting emerging respiratory pathogens with Clamp Peptides: broad-spectrum inhibition of viral entry in 3D human lung models https://t.co/48QvLF0T4F #genetherapy #celltherapy

[Molecular Therapy Family of Journals @MolTherapy]

Antibody Format Matters: A Comparative Analysis of VHH and scFv Domains Reveals Superior In Vivo CAR T Cell Function with VHH Domains https://t.co/LjfiLRGo3u #genetherapy #celltherapy

[Molecular Therapy Family of Journals @MolTherapy]

Therapeutic rescue of pathogenic asparaginyl-tRNA synthetase alleles https://t.co/KmG6MJrH7O #MTNA

[Molecular Therapy Family of Journals @MolTherapy]

Natural Killer Cell-Derived Extracellular Vesicles Reprogram Cellular Human Immunity to Enhance Tumour Cytotoxicity https://t.co/e6kYxPnOd0

[Molecular Therapy Family of Journals @MolTherapy]

Milk-Derived Extracellular Vesicles Loaded with miR-146a-5p as a Novel Therapeutic Strategy for Allergic Airway Inflammation https://t.co/78EvsfRcVK #MTNA