Rare diseases are not so rare: there are 7,000 rare disorders that combined affect 30 million Americans – 1 in 10 of us – and more than half are children. https://t.co/wk4gvdCobH
After a 26-year absence, the primary mosquito that transmits Zika virus, yellow fever and other flaviviruses has been found in Alabama. We're working on a solution! https://t.co/4PpjMjqpzN
There may be no scientific evidence that a person's attitude improves cancer treatments but it can effect mental state and quality of life. https://t.co/4ftws6fd0A
Rare diseases affect more Canadians than all cancers combined, diabetes or cardiovascular disease. Canada has no legal framework for the development of orphan therapies — unlike the United States, which adopted the Orphan Drug Act in 1983. https://t.co/bTL7hZasWy
For many, the acronym "SMA" may be foreign. But for parents of a child with spinal muscular atrophy, a rare but deadly genetic disorder, it is all too real. https://t.co/gPK1CbW0Zr
Cure SMA has a stringent process for determining how to fund research. The news that our research collaborator, Prof. Ken Hodgetts, received a $300,000 grant to move forward on LDN-5178, for which we hold exclusive rights, is truly a breakthrough. https://t.co/XSVELGm9Vl