What would you do if both your children were diagnosed with an ultra #RareDisease affecting fewer than 150 people in the world? And there was no medical treatment available for them?
🧵 read on...
Hot off the press...critical toxicology work for our @US_FDA IND application toward a clinical trial testing ASA for #RareDisease#myotwitter
Adenylosuccinic Acid Is a Non-Toxic Small Molecule In Vitro and In Vivo https://t.co/K59jYcIR5n #mdpipharmaceuticals via @MDPIOpenAccess
So very excited for our research on re-purposed dimethyl fumarate as a treatment for #Duchenne muscular dystrophy to be in @JCI_insight. Thanks to our wonderful collaborators and to @MDAorg and @Telethon_France for funding our research program to further explore this therapy
Today opened @western_health research week and the @AIMSSresearch seminar was a cracker! Congrats to @AIMSSmyopathy members in training who were awarded student poster prizes for their fabulous research: Memphis Calzone, Didier Debrincat @StephKourakis1 and supervisors.
On September 7, we will be observing World Duchenne Day alongside the rest of our community.
To help us raise awareness and funds for research, be sure to buy your own World Duchenne Day tee shirt to wear on Sept. 7.
Purchase here: https://t.co/99rVIZyJwl👕
Cara Timpani @CaraTimpani from @iHealthSportVU presenting in the second session of the VMN Symposium on “Dimethyl fumarate targets the disease interactome and attenuates murine Duchenne muscular dystrophy” VicMuscleNet #myotwitter@AIMSSresearch