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A fascinating read about a promising cell therapy for RPE (Retinal Pigment Epithelium) degeneration such as in age related macular degeneration.
https://t.co/Fmyxzb1ZAX
This interesting study looks at aiming to repair pathogenic allele-specific single-nucleotide mutations using a single round of genome editing.
https://t.co/NJUGXaLzIx
The European Medicines Agency (EMA) has agreed to review a request to approve the investigational CAR T-cell therapy, lisocabtagene maraleucel (liso-cel), for people with pretreated lymphomas.
https://t.co/rmrMY141uq
CAR-T cells are promising for the treatment of cancer but their side effects are a concern. In this study, a team has developed a new CAR T-cell immunotherapy strategy that uses light to activate the immune cells specifically in cancerous regions.
https://t.co/8kFrfCQYcW
This study shows the safety and efficacy of dopaminergic progenitors (DAPs) derived from a clinical-grade human iPSC line. These cells have the potential to replace damaged neurons in Parkinson’s disease.
https://t.co/DD0aXHM4X6
This study identifies roles of autophagy in embryonic stem cell renewal and differentiation and presents an opportunity for new regenerative medicines.
https://t.co/wFeU6XepB4
A nice summary of terminology relating to advanced therapy medicinal products (ATMPs), including gene and cell-based therapies, tissue-engineered products, and combined ATMPs.
https://t.co/2s9EezyPlw
The U.S. Food and Drug Administration (FDA) restarting on-site inspections based on a COVID-19 Advisory Rating system (COVID-19 Advisory Level).
https://t.co/IRbHOAQLvN
The Medicines and Healthcare products Regulatory Agency (MHRA) is making careful preparations for a safe return to normal UK on-site Good Practice (GxP) inspection scheduling.
https://t.co/kBuuZuZr1Z