Announcing Zebronkysen: Amelia & Makenzie receive personalized ASO drug. This milestone would not be possible without the incredible support of the ForeBatten community and the passionate development team.
More information on this exciting news is on https://t.co/PhnooMbTYM
Today is International Batten Disease Awareness Day. To learn more about CLN3 Batten disease and the research we are doing in the @HastingsLab, check out our latest publication. Iโm honored to work with such an amazing team! @MattyStratty22@DrJWeimer@forebatten
Exciting work from the Hastings lab! Fantastic job! @HastingsLab@Wren_Wren@RFUniversity
Open reading frame correction using splice-switching antisense oligonucleotides for the treatment of cystic fibrosis https://t.co/ZOk7WmzQck
Excited to report on our new work using antisense oligonucleotides for cystic fibrosis. @Wren_Wren
Open reading frame correction using antisense oligonucleotides for the treatment of cystic fibrosis caused by CFTR-W1282X https://t.co/4pT5Sg7qiU
Just published our work in Nature Medicine! Thankful to be able to work with such a great group of researchers.
https://t.co/LeFquH4yN4
@HastingsLab@DrJWeimer
Exciting data from the @HastingsLab! Awesome work @Wren_Wren!
#antisense#oligonucleotides
Antisense oligonucleotide-mediated correction of CFTR splicing improves chloride secretion in cystic fibrosis patient-derived bronchial epithelial cells https://t.co/Wd3CaBNzSX
On #RareDiseaseDay, we are most grateful for our recent partnership with Chicago biotech company #Exicure. In collaborating with our Center for Genetic Diseases, we hope to discover successful new therapeutics for #geneticdiseases. https://t.co/lw1UhEoLTe
Such an honor to once again emcee a fundraiser to find a cure for Batten Disease. This is our 9th year. We started in a small banquet room with 60 people. Look at how the support has grown. And it gets us closer to finding a treatment and cure. Learn more: https://t.co/17BIH4lcUB