@CIRMnews is a proud sponsor of the Gene Therapy Initiative Symposium at @UCSDHealth, which bring together researchers and industry experts to share scientific discoveries and boost collaboration to advance cell and gene therapy treatments for patients everywhere. #gtiUCSD
Check out this report from @CherquiLab et al. "Rescue of Alzheimer's disease phenotype in a mouse model by transplantation of wild-type hematopoietic stem and progenitor cells", published in @CellReports#ASGCT2024 https://t.co/oiy4cOU8aK
We are thrilled for our project scientist Anusha to be 1 of 10 researchers receiving a $20,000 grant from @UpliftingAth! This grant will aid her research and support the 1 in 10 Americans diagnosed with a #RareDisease. https://t.co/rp5vTApExh
Backed by a $5M gift from Nancy & Geoffrey Stack Foundation, @UCSanDiego officially launches the Gene Therapy Initiative 🧬. Led by Drs. Cherqui & Muotri, the initiative will fuel research🔬+ gene therapies💉to benefit patients with #Genetics disorders
https://t.co/tTJ0UU3j26
Out now in @CellReports, Dr. Stephanie Cherqui's (@Cherqui_S) lab shows hematopoietic #StemCell transplants can protect against memory loss, neuroinflammation and β-amyloid build-up in a mouse model of #AlzheimersDisease 🧠
https://t.co/pNQwaOGy4U
🎧 NEW PODCAST 🎧 Professor @Cherqui_S is a pioneer in the field of #CRISPR cell and gene therapies. She speaks about her work on curing genetic diseases such as Friedreich's ataxia, obstacles in clinical development, and the future of CRISPR therapies 👉 https://t.co/OqXNAUYqGw
@imp_ax@rafaelabadell @Cherqui_S The phase 1/2 clinical trial has yielded encouraging and favorable outcomes. Additionally, all six participants for this study have received infusions of the gene-edited stem cells as planned. We have no comment on AVROBIO's work though.
Excited to share the FAID reel of 2022! It's a delightful visual summary of our recent conference. Our team has worked hard to make this event happen, and we couldn't be more proud of what we have achieved so far. #ClinicalTrials#GeneTherapy
https://t.co/gi1E28grw4
Professor Stephanie Cherqui of @UCSDMedSchool speaks to us about a prestigious grant from the California Institute for Regenerative Medicine, which will allow her team to bring a new CRISPR therapy for Friedreich’s ataxia to the clinic.
Read more here: https://t.co/XhBEEe5FQU
@CIRMnews We are grateful for the funding opportunity granted by the California Institute for Regenerative Medicine (CIRM) to develop a treatment for Friedreich’s ataxia (FA) patients using CRISPR/Cas9-mediated gene editing technology, a novel ex vivo gene therapy approach.