Cherqui Lab

Lab of Dr. Stephanie Cherqui @UCSDHealth. Developing stem cell and gene therapy strategies for degenerative multi-systemic disorders.

[California Institute for Regenerative Medicine @CIRMnews]

@CIRMnews is a proud sponsor of the Gene Therapy Initiative Symposium at @UCSDHealth, which bring together researchers and industry experts to share scientific discoveries and boost collaboration to advance cell and gene therapy treatments for patients everywhere. #gtiUCSD

[Cell Press @CellPressNews]

Check out this report from @CherquiLab et al. "Rescue of Alzheimer's disease phenotype in a mouse model by transplantation of wild-type hematopoietic stem and progenitor cells", published in @CellReports #ASGCT2024 https://t.co/oiy4cOU8aK

[Cherqui Lab @CherquiLab]

Come checkout our Postdoc Veenita’s poster on Renal Fanconi Sundrome in Cystinosis @WORLDSymposia

[Rafael A. Badell-Grau, PhD @rafaelabadell]

Excited to kick off @WORLDSymposia lysosomal disease conference this year by attending an important @CureSanfilippoF meeting on leveraging data to advance Sanfilippo therapeutic development! #lysosomes #genetherapy #hspc #sanfilippo #mps @UCSDHealth @MPSSociety

[Cherqui Lab @CherquiLab]

We are thrilled for our project scientist Anusha to be 1 of 10 researchers receiving a $20,000 grant from @UpliftingAth! This grant will aid her research and support the 1 in 10 Americans diagnosed with a #RareDisease. https://t.co/rp5vTApExh

[Rafael A. Badell-Grau, PhD @rafaelabadell]

Excited to be at the @MPSSociety 37th Annual Family Conference to present some of my work at @CherquiLab on gene modified HSPC for MPSIIIC! @UCSDHealth #GeneTherapy #StemCells

[Cherqui Lab @CherquiLab]

Backed by a $5M gift from Nancy & Geoffrey Stack Foundation, @UCSanDiego officially launches the Gene Therapy Initiative 🧬. Led by Drs. Cherqui & Muotri, the initiative will fuel research🔬+ gene therapies💉to benefit patients with #Genetics disorders
https://t.co/tTJ0UU3j26

[UC San Diego Health Sciences @UCSDHealthSci]

Out now in @CellReports, Dr. Stephanie Cherqui's (@Cherqui_S) lab shows hematopoietic #StemCell transplants can protect against memory loss, neuroinflammation and β-amyloid build-up in a mouse model of #AlzheimersDisease 🧠

https://t.co/pNQwaOGy4U

[Giulio Maria Pasinetti, MD, PhD @IcahnCMIN]

EXCITING STUDY! In new proof-of-concept study, Priyanka Mishra, Stephanie Cherqui et al. show #StemCell transplants may also be promising therapeutic against #AlzheimersDisease. @CherquiLab @ucsdstemcell @ljiresearch @CellReports
https://t.co/eY1SqlYiea
https://t.co/bfUeGTqFa7

[Rafael A. Badell-Grau, PhD @rafaelabadell]

Honoured to have been awarded one of the @ASGCTherapy 2023 outstanding poster award for my abstract on my work in the @CherquiLab @UCSDHealth on Hematopoeitic #stemcell #genetherapy for MPSIIIC funded by @MPSSociety & @CureSanfilippoF

[Cherqui Lab @CherquiLab]

Great week for the Cherqui lab ⁦@ASGCTherapy⁩ presenting our latest work! #stemcell #genetherapy ⁦@UCSDHealth⁩ https://t.co/i58WnFezHn

[Rafael A. Badell-Grau, PhD @rafaelabadell]

Happy to be back presenting a poster at the @ASGCTherapy annual meeting on my work at @CherquiLab on #stemcell #GeneTherapy for Sanfilippo C funded by @MPSSociety & @CureSanfilippoF. Poster No. 649

[Synthego @Synthego]

🎧 NEW PODCAST 🎧 Professor @Cherqui_S is a pioneer in the field of #CRISPR cell and gene therapies. She speaks about her work on curing genetic diseases such as Friedreich's ataxia, obstacles in clinical development, and the future of CRISPR therapies 👉 https://t.co/OqXNAUYqGw

[Cherqui Lab @CherquiLab]

@imp_ax @rafaelabadell @Cherqui_S The phase 1/2 clinical trial has yielded encouraging and favorable outcomes. Additionally, all six participants for this study have received infusions of the gene-edited stem cells as planned. We have no comment on AVROBIO's work though.

[Cherqui Lab @CherquiLab]

Thank you @rafaelabadell for representing our lab at @WORLDSymposia 2023. Also, a special acknowledgement goes out to @MPSSociety and @CureSanfilippoF for your fellowship supports!

[Rafael A. Badell-Grau, PhD @rafaelabadell]

I am very happy and grateful to have received the fellowship award from the @CureSanfilippoF to continue my work investigating the use of #stemcell #genetherapy to treat Sanfilippo type C in the @CherquiLab @UCSDHealth

[Cherqui Lab @CherquiLab]

Excited to share the FAID reel of 2022! It's a delightful visual summary of our recent conference. Our team has worked hard to make this event happen, and we couldn't be more proud of what we have achieved so far. #ClinicalTrials #GeneTherapy
https://t.co/gi1E28grw4

[FA Research Alliance @CureFA_org]

Congratulations to all of the recipients, including @AquilanoKatia, @Cherqui_S, and @USFHealth
Together, we will #SlowStopReverse and #CureFA

[CRISPR Medicine @CrisprMedicine]

Professor Stephanie Cherqui of @UCSDMedSchool speaks to us about a prestigious grant from the California Institute for Regenerative Medicine, which will allow her team to bring a new CRISPR therapy for Friedreich’s ataxia to the clinic.

Read more here: https://t.co/XhBEEe5FQU

[Cherqui Lab @CherquiLab]

https://t.co/PioTn7HPnU
#CIRM #UCSD #CureFA

[Cherqui Lab @CherquiLab]

@CIRMnews We are grateful for the funding opportunity granted by the California Institute for Regenerative Medicine (CIRM) to develop a treatment for Friedreich’s ataxia (FA) patients using CRISPR/Cas9-mediated gene editing technology, a novel ex vivo gene therapy approach.

[Cherqui Lab @CherquiLab]

Your support helps greatly in our effort to transition this project from bench to bedside.