CIRM celebrates a major milestone—the first therapy funded by California taxpayer dollars is now approved by the @FDA. This new gene therapy is a one-time therapy developed by @RocketPharma to treat the rare childhood disease LAD-I. Read full story: https://t.co/ByJUkgYlcA
Braingeneers, a team spanning UC Santa Cruz, UCSF, UCSB, Stanford & WashU, is combining AI and human brain organoids to study neural circuits and disease. Building on CIRM-funded organoid research, the work also raises key ethical questions.
https://t.co/Oafk5onTxG
CIRM-funded research led by Dr. Steven Deeks at @ucsfhealth found an investigational CAR-T therapy for HIV was safe in an early first-in-human trial. Early results suggest it may delay viral rebound or extend suppression. More: https://t.co/hVg2xtAQOG
On the @ucsdstemcell podcast, Dr. Sheldon Morris, Director of the Sanford Stem Cell Clinical Center, discussed how collaboration with @UCSDHealth, industry, and researchers drives discoveries in stem cells, regenerative medicine, and gene therapies. https://t.co/q90FbCcBFE
3M+ Californians live with knee #osteoarthritis. With $12M from CIRM, @genascence is advancing investigational gene therapy GNSC-001, designed to reduce inflammation, pain, and cartilage damage. Early data are promising; a larger trial is next. Read more: https://t.co/JZCmUaRIq1
@USCEye and @KeckMedicineUSC are launching a CIRM-funded Phase 2b trial of a stem cell-derived retinal implant for advanced #dryAMD. The study will test whether it can safely replace damaged retinal cells and improve vision. https://t.co/J1lCDVvsr9
CIRM’s largest research budget to date is an investment in Californians and the power of regenerative medicine to improve lives. In 20 years, CIRM funding has supported 100+ clinical trials for diseases without cures and expanded access. Full story: https://t.co/T5TMh9c2cp
New @UCSFstemcell research suggests CAR-T cell therapy may offer a new approach to HIV treatment. In a CIRM-funded trial led by Dr. Steve Deeks, engineered immune cells suppressed HIV in two patients. Hear more June 25 at 10:30 AM (PT): https://t.co/j5AYdULdRd
Hear from Genascence's founder and CEO, Tom Chalberg, on June 25 at 10:30 AM (PT), who will share an update on GNSC-001, a potential first-in-class gene therapy for knee osteoarthritis, and the progress of the CIRM-funded DONATELLO clinical trial. Watch on https://t.co/qBqOOLvOQL
Join us for Closer to Cures on June 25 at 10:30 AM PT. Hear CIRM awardees Dr. Tom Chalberg and Dr. Steve Deeks share updates on clinical trials in knee osteoarthritis and HIV. Watch live on CIRM’s YouTube: https://t.co/TNnTqaOe6T
When Tiffany Wang arrived at USC as a first-generation student, she was searching for belonging. Four years later, she's graduating as an award-winning researcher, student leader, COMPASS Fellow, and QuestBridge Scholar.
Read more here: https://t.co/occjvAOrWv
CIRM invested $2M to support @UCLAstemcell's new Center for Advanced Biotherapies, helping expand cell and gene therapy manufacturing, speed early clinical trials, and build California’s regenerative medicine future. https://t.co/BHVhHfYbTP
Finding a #ClinicalTrial in California is now easier. CIRM’s new dashboard helps patients quickly search active cell and gene therapy trials at nine CIRM-funded Alpha Clinics across the state. Learn more: https://t.co/wy2ZHO4sl1
CIRM’s RAPID funding opportunity aims to speed development of platform-based genetic therapies for rare diseases. The RFA is available for view and the mandatory consultation period is open. Interested applicants must schedule a consultation. Learn more at https://t.co/jUahwK4fCp
California voters helped create a stem cell research ecosystem supporting #research in 85+ diseases and nearly 1.5K grants. On the @ucsdstemcell reGEN Podcast, CIRM's CEO explains how that vote made #California a global leader in regenerative medicine: https://t.co/OLPgAgXqyq
At @UCLAHealth California Center for Rare Diseases, progress is accelerating for patients with complex genetic conditions. From coordinated specialty care to promising gene therapy research, including work led by Dr. Donald Kohn, hope is growing. https://t.co/tDHGzeL49H
On the @ucsdstemcell reGEN Podcast, @cityofhope's Dr. Leo Wang highlights how CIRM Alpha Clinics is helping bring cutting-edge therapies to more patients across California through collaboration, access, and innovation. Listen to the full episode. https://t.co/Qy25G96G5m
Dr. Stephanie Cherqui and her team at @UCSDHealth developed a CIRM-supported stem cell-based genetic therapy that changed Jordan Janz’s life. Now, CIRM’s RAPID initiative aims to build on breakthroughs like this to help more people with rare diseases: https://t.co/CMURMsEPug
https://t.co/L1WtCq7Edv Tune in for our latest reGEN podcast 🎙️ interview with Sheldon Morris, MD, MPH, director of the Sanford Stem Cell Clinical Center, as we discuss his past and current research, the @CIRMnews Alpha Clinic & clinical trials. #stemcells#medtwitter#podcast
CIRM Vice Chair Maria Gonzalez Bonneville joined after her father’s Parkinson’s diagnosis. Now she chairs CIRM’s Accessibility & Affordability Working Group to help ensure CIRM-backed therapies reach all Californians. https://t.co/BkdaUuhTCu
Clinical trials don’t move forward without people. For #ClinicalTrialsDay, we’re honoring the patients who make progress possible. CIRM supports 100+ clinical trials and a statewide Alpha Clinics network to expand access across California. Read more: https://t.co/f66ofNgypx