Intellia once again leads the way with the first-ever in vivo CRISPR-based gene editing therapy cleared to enter late-stage clinical development!!!
Proud of the entire team on this achievement. #CRISPR#OneIntellia#ATTR
#ATTR News: @US_FDA cleared Intellia’s NTLA-2001 IND application to enter late-stage clinical development for the treatment of #transthyretinamyloidosis with cardiomyopathy: https://t.co/q1m2h9SANH
NTLA-2001 is the first-ever investigational in vivo therapy cleared by FDA to enter a Phase 3 trial. #CRISPR #GeneEditing
Let’s GO!!!
➡️The word “hold” is not in Intellia’s vocabulary!
Intellia Announces FDA Clearance of IND Application for NTLA-2002, an In Vivo CRISPR-Based Investigational Therapy for the Treatment of Hereditary Angioedema (HAE)
$NTLA $VERV $BEAM https://t.co/zzi4lCo2RW
Congrats to @intelliatx and everyone that has played a part in the advancement of CRISPR to get it to this point! This is a significant milestone for the entire gene editing field🎉 https://t.co/XfglmnSZjU
#HAE News: Intellia has been awarded the Innovation Passport in the U.K. by @MHRAgovuk for NTLA-2002, the company’s investigational #genomeediting treatment for #hereditaryangioedema. Learn more: https://t.co/6iM67LbdXB
Intellia CEO, John Leonard, reflects on Intellia’s recent growth, accomplishments and the journey that lies ahead: https://t.co/WBZAVCfVZA #CRISPR#genomeediting#OneIntellia
“A big part of this is education.”
@intelliatx Chief Business Officer Derek Hicks emphasizes that the cell and gene sector needs to better educate regulators and the public to support systems for successful CMC. #CGSOTI23
CRISPR has delivered on a key aspect of its promise as a platform technology: going from disease 1 to disease 2 requires changing only 20 nt in an RNA.
This is exactly what @intelliatx just did: the HAE data look as good as the TTR ones.
YAY+BRAVO!
https://t.co/kzyze2P2Dy
Today’s #HAE and #ATTR data support the modularity of Intellia’s industry-leading #genomeediting platform. Incredibly proud to be part of #OneIntellia!
$NTLA announced today the @US_FDA has granted orphan drug designation for our in vivo #CRISPR/Cas9 genome editing candidate, NTLA-2002, for the treatment of hereditary angioedema (#HAE). Learn more: https://t.co/lNy64hG13W
Congratulations @intelliatx! Learn more about NTLA-2002 on our website and at an upcoming presentation at the 2022 Bradykinin Symposium
https://t.co/QpLALzJmEP
https://t.co/psTSIVFJtQ
#HAE#CRISPR#ONEintellia
$NTLA announces upcoming date for the presentation of interim clinical data for our second systemically administered in vivo #CRISPR candidate: https://t.co/SZQQXWzbKT
I’m so proud of our team, and today’s APOLLO-B announcement which represents the next step in @Alnylam’s journey both in building our TTR franchise and toward achieving our P5x25 corporate vision of becoming a leading biopharma company. #RNAitherapeutics#siRNA