The first journal devoted to the science, technology and clinical application of human gene therapy. Established in 1990. Editor-in-Chief: Terry Flotte.
NEW WEBINAR! On 11/13, our experts discuss strategies for implementing iPSC-derived assays in gene therapy development pipelines, with a focus on assay design, quantifiable potency metrics, and considerations for regulatory alignment. REGISTER: https://t.co/Se8eU6ysLb #Ncardia
Join GEN for The State of CRISPR and Genome Editing virtual summit on June 11! Hear from experts like Feng Zhang and Fyodor Urnov. Don't miss out—register for free today! https://t.co/5OVfUwcN1B
Are you in New Orleans for the 2025 ASGCT Annual Meeting? Stop by Booth #1350 to catch up with the Mary Ann Liebert, GEN, and Inside Precision Medicine teams! Pick up your copies of Human Gene Therapy, GEN, CRISPR Journal, and more at this year's meeting. #ASGCT2025
Read the April issue of Human Gene Therapy with your free digital edition, available now during the @ASGCTherapy Annual Meeting: https://t.co/JZoIDUHQPP
Read the April issue of Human Gene Therapy with your free digital edition, available now during the @ASGCTherapy Annual Meeting: https://t.co/JZoIDUHQPP
Online now: Meta-Analysis and Optimization of the In Vitro Immortalization Assay for Safety Assessment of Retroviral Vectors in #GeneTherapy: https://t.co/ds4zgsiP8T
Tomorrow -- @GENbio Webinar: Making Protein Therapeutics Affordable and Accessible Using Fully-Connected Continuous Biomanufacturing. 8:00 am PT, 11:00 am ET, 17:00 CEST. Register free now at: https://t.co/moNkPGmkYV
Prediction of Adeno-Associated Virus Fitness with a Protein Language-Based Machine Learning Model... Read the Free Access research article by Christian Mueller and coauthors from @sanofi : https://t.co/lgkadJQeUl
Machine Learning Model to Predict the Fitness of AAV Capsids for #GeneTherapy. Read the Free Access research article by Christian Mueller and coauthors from @sanofi : https://t.co/lgkadJQeUl
Prediction of Adeno-Associated Virus Fitness with a Protein Language-Based Machine Learning Model... Read the Free Access research article by Christian Mueller and coauthors from @sanofi : https://t.co/lgkadJQeUl
Machine Learning Model to Predict the Fitness of AAV Capsids for #GeneTherapy. Read the Free Access research article by Christian Mueller and coauthors from @sanofi : https://t.co/lgkadJQeUl
New articles from the February Issue, free for a limited time -- Directed Evolution of AAV9 for Efficient Gene Expression in Cardiomyocytes In Vitro and In Vivo: https://t.co/2HpyoM9UPj
New articles from the February Issue, free for a limited time -- Current and Emerging Issues in Adeno-Associated Virus Vector-Mediated Liver-Directed #GeneTherapy: https://t.co/OBEo6ngY9S
New articles from the February Issue, free for a limited time -- Thrombotic Microangiopathy Associated with Systemic Adeno-Associated Virus Gene Transfer: Review of Reported Cases. https://t.co/Mt7jV2nk9c
Call for Papers -- Special Issue on #GeneTherapy for Diseases of the Respiratory System. Deadline for Manuscript Submissions: April 25, 2025. Submit Today! https://t.co/QMvDzdMl8n