Human Gene Therapy

The first journal devoted to the science, technology and clinical application of human gene therapy. Established in 1990. Editor-in-Chief: Terry Flotte.

[Human Gene Therapy @HGTJournal]

Join our webinar on 11/13 to explore iPSC-derived assays in gene therapy: assay design, quantifiable potency, and regulatory insights. Register now: https://t.co/eBGlUxBmJJ #GeneTherapy #iPSC #Webinar #Biotech #Ncardia

[Human Gene Therapy @HGTJournal]

FREE WEBINAR! Advancing Gene Therapy Potency Testing with iPSC-Based Systems. REGISTER: https://t.co/syJjnCeV74 #Ncardia #genetherapy #assays #therapyvectors #freewebinar

[Human Gene Therapy @HGTJournal]

NEW WEBINAR! On 11/13, our experts discuss strategies for implementing iPSC-derived assays in gene therapy development pipelines, with a focus on assay design, quantifiable potency metrics, and considerations for regulatory alignment. REGISTER: https://t.co/Se8eU6ysLb #Ncardia

[Human Gene Therapy @HGTJournal]

Join GEN for The State of CRISPR and Genome Editing virtual summit on June 11! Hear from experts like Feng Zhang and Fyodor Urnov. Don't miss out—register for free today! https://t.co/5OVfUwcN1B

[Human Gene Therapy @HGTJournal]

Are you in New Orleans for the 2025 ASGCT Annual Meeting? Stop by Booth #1350 to catch up with the Mary Ann Liebert, GEN, and Inside Precision Medicine teams! Pick up your copies of Human Gene Therapy, GEN, CRISPR Journal, and more at this year's meeting. #ASGCT2025

[Human Gene Therapy @HGTJournal]

Read the April issue of Human Gene Therapy with your free digital edition, available now during the @ASGCTherapy Annual Meeting: https://t.co/JZoIDUHQPP

[Human Gene Therapy @HGTJournal]

Read the April issue of Human Gene Therapy with your free digital edition, available now during the @ASGCTherapy Annual Meeting: https://t.co/JZoIDUHQPP

[Human Gene Therapy @HGTJournal]

Online now: Creating New Cis-Regulatory Elements of HBD to Reactivate Delta-Globin: https://t.co/vbHni6U6B6

[Human Gene Therapy @HGTJournal]

Online now: @BeamTx Results Show First Genetic Correction of Disease-Causing Mutation: https://t.co/Mij0Uy8g4h

[Human Gene Therapy @HGTJournal]

Online now: Meta-Analysis and Optimization of the In Vitro Immortalization Assay for Safety Assessment of Retroviral Vectors in #GeneTherapy: https://t.co/ds4zgsiP8T

[Human Gene Therapy @HGTJournal]

Tomorrow -- @GENbio Webinar: Making Protein Therapeutics Affordable and Accessible Using Fully-Connected Continuous Biomanufacturing. 8:00 am PT, 11:00 am ET, 17:00 CEST. Register free now at: https://t.co/moNkPGmkYV

[Human Gene Therapy @HGTJournal]

Identifying a Novel Factor in Canavan Disease Pathogenesis -- Read the Open Access article now: https://t.co/4bkhWpmHC4

[Human Gene Therapy @HGTJournal]

Prediction of Adeno-Associated Virus Fitness with a Protein Language-Based Machine Learning Model... Read the Free Access research article by Christian Mueller and coauthors from @sanofi : https://t.co/lgkadJQeUl

[Human Gene Therapy @HGTJournal]

Machine Learning Model to Predict the Fitness of AAV Capsids for #GeneTherapy. Read the Free Access research article by Christian Mueller and coauthors from @sanofi : https://t.co/lgkadJQeUl

[Human Gene Therapy @HGTJournal]

Prediction of Adeno-Associated Virus Fitness with a Protein Language-Based Machine Learning Model... Read the Free Access research article by Christian Mueller and coauthors from @sanofi : https://t.co/lgkadJQeUl

[Human Gene Therapy @HGTJournal]

Machine Learning Model to Predict the Fitness of AAV Capsids for #GeneTherapy. Read the Free Access research article by Christian Mueller and coauthors from @sanofi : https://t.co/lgkadJQeUl

[Human Gene Therapy @HGTJournal]

New articles from the February Issue, free for a limited time -- Directed Evolution of AAV9 for Efficient Gene Expression in Cardiomyocytes In Vitro and In Vivo: https://t.co/2HpyoM9UPj

[Human Gene Therapy @HGTJournal]

New articles from the February Issue, free for a limited time -- Current and Emerging Issues in Adeno-Associated Virus Vector-Mediated Liver-Directed #GeneTherapy: https://t.co/OBEo6ngY9S

[Human Gene Therapy @HGTJournal]

New articles from the February Issue, free for a limited time -- Thrombotic Microangiopathy Associated with Systemic Adeno-Associated Virus Gene Transfer: Review of Reported Cases. https://t.co/Mt7jV2nk9c

[Human Gene Therapy @HGTJournal]

Call for Papers -- Special Issue on #GeneTherapy for Diseases of the Respiratory System. Deadline for Manuscript Submissions: April 25, 2025. Submit Today! https://t.co/QMvDzdMl8n