Congrats to Ahmed (who now holds the lab record for most co-authored undergraduates on a single manuscript) and to the Julia Liu and Eric Batchelor labs: https://t.co/C4hq1nFO8G
Excited to share our new paper on LNP delivery of antisense gapmers for FSHD.
Repeated systemic LNP-gapmer treatment reduced DUX4, improved muscle function, and ameliorated pathology in an FSHD mouse model.
Congrats to Saeed and all collaborators!
https://t.co/pW58AR4AjW