Do you know an ASGCT member who has supported the translation of #GeneTherapy and #CellTherapy from preclinical to clinical research settings? Submit a nomination for the inaugural Jerry Mendell award. https://t.co/q8zfvlydio
At SRPT, we’re on an urgent mission to engineer precision genetic medicines to reclaim futures otherwise stolen by #rarediseases. Learn about our science, get to know our team, and meet the patients and families who inspire our mission: https://t.co/Fj9GrqIHK8
We have officially launched our new website! Thank you to the patients and families who generously shared their time and stories.
Take an inside look at how SRPT infused its corporate brand with urgency and optimism on behalf of patients: https://t.co/O9UHj3ZQs4
#ASGCTYearInReview: #GeneTherapy to treat #Duchenne muscular dystrophy shows “very encouraging” results in nine-month updates on a cohort of four boys. Updated data reveals 81.2 percent increase in dystrophin protein expression. https://t.co/zieK8zT3iN
#BREAKING: Today, we announced a strategic licensing agreement with @Roche for SRP-9001, our investigational #genetherapy candidate for #Duchenne#musculardystophy, in countries outside the US
Learn more: https://t.co/4DDT1kYrzX #SRPT
Columbus is the top city in the Midwest and No. 2 in the nation for finding a job in the new year, according to a ranking from Forbes. https://t.co/klztY1Noto