UK Platform for Nucleic Acid Therapies- UPNAT

Creating a national network of experts/stakeholders to facilitate & promote the development of Nucleic Acid Therapies for patients with rare diseases in the UK

[UK Platform for Nucleic Acid Therapies- UPNAT @UpNAT_node]

Today, on #RareDiseaseDay, we are happy to share the @DHSCgovuk newly published 2025 England Rare Disease action plan - exciting work ahead for the @UpNAT_node!
https://t.co/K4VCn0cKPn #RareDiseaseDay #RareDiseaseDay2025 #RareDisease

[UK Platform for Nucleic Acid Therapies- UPNAT @UpNAT_node]

12 PhDs on Antisense oligonucleotide #research to foster the full therapeutic potential of antisense technology across tissues https://t.co/X5zLUkVG8T
11 posts across Europe, the other at UCL under @UpNAT_node Director Haiyan Zhou @lab_zhou

[UK Platform for Nucleic Acid Therapies- UPNAT @UpNAT_node]

UPNAT Director Haiyan Zhou is keynote speaker at the upcoming Cambridge Chem&Bio Seminar on Nucleic Acid Research. @lab_zhou @UpNAT_node
Space is available on 14 Dec "whether you're a student, researcher, or simply curious about the field", book here: https://t.co/WcajdMoLZv

[UK Platform for Nucleic Acid Therapies- UPNAT @UpNAT_node]

Congrats to Carlo Rinaldi @rinaldi_ca, awarded title of Professor of Molecular & Translational Neuroscience @UniofOxford Institute of Developmental & Regenerative Medicine.
Carlo is @UpNAT_node PI, streamlining NAT clinical trials & regulatory approval. https://t.co/tRCk38ky5z

[UK Platform for Nucleic Acid Therapies- UPNAT @UpNAT_node]

The Oxford-Harrington Rare Disease Centre has announced inaugural 2024 Rare Disease Scholar award recipients, which includes two members of the @UpNAT_node team. Well done Haiyan Zhou and Carlo Rinaldi on this notable achievement! @OHRareDisease @lab_zhou @rinaldi_ca @RDRUKHub

[UK Platform for Nucleic Acid Therapies- UPNAT @UpNAT_node]

Join the @UpNAT_node team!
Applications for the Child Health Research (CHR) PhD Studentships for 25/26 are open. Deadline for students to apply is 09:00 Friday 13th December.
https://t.co/hzSqrYDSrx

[UK Platform for Nucleic Acid Therapies- UPNAT @UpNAT_node]

An interesting paper to contextualise the recent published guidelines by the Dutch Center for RNA Therapeutics
https://t.co/sFDmf7lHEj @oligogirl @LaufferMarlen @roon_mom #raredisease

[Marlen Lauffer @LaufferMarlen]

@oligogirl @timyu @UpNAT_node @BeijerDanique @aubriesoucy The guidelines are accompanied by training videos and test variants for practicing assessments. All videos are available via the N1C YouTube Channel. https://t.co/oT3wco4hji

[UK Platform for Nucleic Acid Therapies- UPNAT @UpNAT_node]

Impressive work by the Dutch Center for RNA Therapeutics! Thanks to @LaufferMarlen for the opportunity to participate in this ASO guideline development, with @UpNAT_node co-authors @aliceedavidson and @MinaRyten https://t.co/S7HEwtVbfR #DCRT

[UK Platform for Nucleic Acid Therapies- UPNAT @UpNAT_node]

We shared the excitement as Haiyan Zhou @lab_zhou presented an update on her research as Harrington Scholar @HarringtonDI_UH.
And appreciated the introduction to our @UpNAT_node!
#OxfordHarrington2024 @OHRareDisease @RDRUKHub #RareDisease

[UK Platform for Nucleic Acid Therapies- UPNAT @UpNAT_node]

UPNAT Node partner Prof Carlo Rinaldi chairs an excellent session at the #OxfordHarrington2024 Rare Disease Centre Symposium. Full agenda here: https://t.co/HeZHCRs05A
@rinaldi_ca @OHRareDisease @UniofOxford @UpNAT_node

[UK Platform for Nucleic Acid Therapies- UPNAT @UpNAT_node]

Excellent speakers lined up for the Oxford-Harrington Rare Disease Centre  Symposium later this month (including @UpNAT_node Director Haiyan Zhou)
Registration is open:
https://t.co/HeZHCRs05A
#RareDiseases @lab_zhou @OHRareDisease

[Rare Disease Research UK @RDRUKHub]

📢Our 2nd Annual Conference is happening on 25th March 2025! Mark your calendars and join us in #Manchester

🔔Stay tuned for more updates!

#RDRUKcon #RareDiseaseResearch #raredisease #Livingrare #hopeforrare

[Oligonucleotide Therapeutics Society @OTSociety]

Join us for an insightful webinar on "A Nucleic Acid Approach to Antibody Therapeutics" on July 18th.

Dr. John Chaput will explore innovative pathways for democratizing antibody therapeutics using threomers.

Register now: https://t.co/iE5GjinQKQ

#ots #webinar #nucleicacid

[UK Platform for Nucleic Acid Therapies- UPNAT @UpNAT_node]

Join the @UpNAT_node team! Now hiring: our candidate will have a PhD degree in biomedical sciences or closely related areas, with strong knowledge & skillset in bioinformatics. Preclinical RNA therapy drug development (ASO, siRNA, mRNA) are highly desired. https://t.co/QTKVUOtMoR

[UK Platform for Nucleic Acid Therapies- UPNAT @UpNAT_node]

Buzzing crowd at yesterday's Genomics England Research Summit, where @MinaRyten contributed to the "Therapeutic Innovations and Trials" session with an introduction to our @UpNAT_node.
@GenomicsEngland #RareDisease #gers2024

[UK Platform for Nucleic Acid Therapies- UPNAT @UpNAT_node]

UPNAT Director Haiyan Zhou @lab_zhou will be speaking tomorrow alongside UK DRI Director Mina Ryten @MinaRyten at the @GenomicsEngland Summit about the @UpNAT_node and enhancing rare disease treatment: https://t.co/xwLs2mFl9Z

[UK Platform for Nucleic Acid Therapies- UPNAT @UpNAT_node]

Now to build on the momentum of the recent @UpNAT_node Symposium, with the help of our partners across the UK and beyond.
With special thanks to @OTSociety who supported PPIE at the event with their generous grant: https://t.co/Lc2Zf5NOoU

[UK Platform for Nucleic Acid Therapies- UPNAT @UpNAT_node]

Join the @UpNAT_node team! Now hiring: our candidate will have a PhD degree in biomedical sciences or closely related areas, with strong knowledge & skillset in bioinformatics. Preclinical RNA therapy drug development (ASO, siRNA, mRNA) are highly desired. https://t.co/QTKVUOtMoR

[UK Platform for Nucleic Acid Therapies- UPNAT @UpNAT_node]

We enjoyed excellent participation from the audience at last week's @UpNAT_node Symposium. Our two panels (1- target selection for #raredisease, and 2- #clinicaltrials and regulatory pathway) in particular generated thoughtful & useful discussion.
@RDRUKHub @The_MRC @NIHRresearch