The FDA and Glafabra Therapeutics will meet face-to-face in July on clinical trial plans for GT-GLA-S03, a gene therapy for Fabry disease. https://t.co/jE0w8XKIXa
Check out my latest article: PROPOSED LEGISLATIVE INITIATIVE: EXTENDING INVESTIGATIONAL DEVICE EXEMPTION (IDE) COVERAGE TO CELL AND GENE THERAPIES https://t.co/lNHAoLpcHE via @LinkedIn
The FDA has granted orphan drug status to GT-GLA-S03, a cell therapy for Fabry disease that aims to provide a long-lasting enzyme supply. https://t.co/p1cxVTct1G
@FabDiseaseNews Excited to be bringing a new therapy option to Fabry patients - one visit every 5 years for infusion with our therapy = 130x infusion visits with standard of care
I'll be speaking at Wilson Sonsini Entrepreneur & Investor Life Science Summit 2026 on Mar 12 - 13, 2026. I would love to see you there!🎉🎉
Register here: https://t.co/ciBYpm4LgI
#e&isummit2026 - via #Whova Event Platform
https://t.co/XsSfOSbVVM
Check out my latest article: LVV and AAV are in their infancy - Don’t doubt their ability to take market share like antibody Abs have!!! https://t.co/hMpZV3o5du via @LinkedIn
Come check out our Pitch at 2025 Entrepreneur & Investor Life Sciences Summit Presented by Wilson Sonsini. #2025e&isummit - via #Whova event app
AARS1 Therapeutics - Variations in AARS1 gene can cause Charcot-Marie-Tooth disease, and Developmental and Epileptic Encephalopathy. See website to learn more: https://t.co/jlw2emsYC7
CTNNB1 Therapeutics - A beta-catenin whose pathogenic variants can cause Severe intellectual disability-progressive spastic diplegia syndrome and various cancers. See Devinebio website to learn more: https://t.co/6A7F0RUHGZ