Bone marrow transplants could offer a new way to treat mitochondrial diseases like Friedreich’s ataxia. A @StanfordMed study in @NatComms showed donor immune cells delivered healthy mitochondria to failing heart & brain cells, improving symptoms in mice. https://t.co/jpN00026ga
ACMG recognizes Natalia Gomez-Ospina, MD, PhD with the 2024 #ACMGFoundation Dr. Michael S. Watson Genetic and Genomic Medicine Innovation Award. She is an Assistant Professor of Pediatrics (Genetics) @StanfordMed. https://t.co/a8di71etPS #ACMGMtg24@CdcmStanford@StanfordChild
Exceptional @KeystoneSymp on Precision Genome Engineering last week
Speaks to value of *in-person interaction* to learn & stimulate new ideas
Here with A. Kwilas, J. Doudna, N. Gomez-Ospina, & @UrnovFyodor
👏M. Porteus & L. Sepp-Lorenzino for organizing
Improved engraftment and therapeutic efficacy by human genome-edited hematopoietic stem cells with Busulfan-based myeloablation https://t.co/Lf6LXWFPsG
https://t.co/iwgXwEOYud
For women in science. Awards are meant to showcase great accomplishment and also to inspire others to follow in their footsteps.
Scientists from @UTSWNews successfully employed a new type of #genetherapy to treat mice with #Duchenne#MuscularDystrophy (#DMD), utilizing #CRISPR-Cas9-based tools to restore dystrophin protein that is missing in many DMD patients. https://t.co/DvgzaQNcgf
IND Clearance Received for Sickle Cell Disease Gene Editing Clinical Trial. Congratulations to CDCM Co-Director, Matthew Porteus and the team at the CDCM for this great achievement.#sicklecell#cdcm @cirm @graphitebio@stanfordmed Read more about it here: https://t.co/qwpgU8QJAN
The first shot of the #mRNA#COVID19 vaccine, approved by the @US_FDA Friday evening, was administered to an intensive care nurse at @NorthwellHealth this morning. https://t.co/wbyIo6GtI7