๐๐ฎ๐ฝ๐ฝ๐ ๐ช๐ผ๐ฟ๐น๐ฑ ๐๐ต๐ผ๐ฐ๐ผ๐น๐ฎ๐๐ฒ ๐๐ฎ๐!๐ซ
In a world that can sometimes feel rough, a few grams of finesse make all the difference. Taking a small sweet break today.
#WorldChocolateDay
Attending tomorrowโs session:
โCan AI Make You a Better Negotiator?โ
with Jรฉrรดme Duberry and Claude Bruderlein (Harvard & Geneva Graduate Institute).
In rare disease negotiations with authorities and companies, understanding how AI can improve preparation and decision-making is becoming increasingly relevant.
#AI #Negotiation #RareDisease
๐๐ฎ๐ฝ๐ฝ๐ ๐๐ป๐ฑ๐ฒ๐ฝ๐ฒ๐ป๐ฑ๐ฒ๐ป๐ฐ๐ฒ ๐๐ฎ๐, ๐๐น๐ด๐ฒ๐ฟ๐ถ๐ฎ!๐ฉ๐ฟ
On this special day, I want to express my deep gratitude to this great country that has welcomed me for many years.
My first missions in Algeria took place during very difficult times in the mid-nineties, for Gaucher Disease yet I was met with incredible trust and friendship.
None of this would have been possible without my dear friend, the late Dr. Madjid Ben Mansour, whose vision and commitment opened the way for treating patients with rare diseases. I will always be grateful to him.
I also want to warmly thank Minister Amor Tou, and Ms Krim โ daughter of one of the great heroes of independence โ and later all the dedicated hematologists who worked with us on PNH and other rare diseases.
Algeria has always been a country of human warmth.
#Carthagenetics #rarediseases #orphandrug
๐๐ฎ๐ฝ๐ฝ๐ ๐ฐ๐๐ต ๐ผ๐ณ ๐๐๐น๐ ๐๐ผ ๐ฎ๐น๐น ๐ผ๐๐ฟ ๐๐บ๐ฒ๐ฟ๐ถ๐ฐ๐ฎ๐ป ๐ณ๐ฟ๐ถ๐ฒ๐ป๐ฑ๐ ๐ฎ๐ป๐ฑ ๐ฝ๐ฎ๐ฟ๐๐ป๐ฒ๐ฟ๐! ๐บ๐ธ
On this special day, I want to express my heartfelt gratitude to the many American companies that have trusted me for years. Without the Orphan Drug Act of 1983, none of this would have been possible. This landmark law opened the door to innovation and gave hope to millions of patients living with rare diseases.
I also want to thank the brilliant researchers who continue to drive progress every day.
A sincere thank you to:
๐๐๐๐ฅ๐๐๐๐ก, ๐๐๐๐๐ฅ๐๐ข๐ก, ๐๐๐๐ซ๐๐ข๐ก, ๐๐๐ก๐ฌ๐๐๐ , ๐๐ ๐๐๐จ๐ฆ, ๐๐ฉ๐๐ซ๐๐ฆ, ๐๐๐ข๐๐๐ก, ๐๐๐ข๐ ๐๐ฅ๐๐ก, ๐๐๐๐๐ฃ๐๐๐ฅ๐, ๐๐๐๐ ๐๐ฅ, ๐๐ก๐ข๐๐๐, ๐๐ก๐ญ๐ฌ๐ฉ๐๐ก๐ง, ๐๐ข๐๐๐ฅ๐ซ/๐ฃ๐๐๐ญ๐๐ฅ, ๐๐๐ก๐ญ๐ฌ๐ ๐, ๐๐ก๐ฆ๐ ๐๐, ๐ ๐ข๐๐๐ฆ, ๐ก๐ฃ๐ฆ, ๐ฃ๐ง๐, ๐ฅ๐๐ฃ๐ง๐ข๐ฅ, ๐ฅ๐๐๐๐ก๐๐ฅ๐ข๐ก, ๐ฅ๐๐๐๐ก๐ซ๐๐๐ข, ๐ฆ๐จ๐๐๐ ๐ฃ๐ข, ๐ฆ๐ง๐๐ ๐๐๐ก๐, ๐ง๐๐ง, ๐จ๐๐ง๐ฅ๐๐๐๐ก๐ฌ๐ซ, ๐ฉ๐ง๐๐ฆ๐ฆ๐, ๐ญ๐ข๐๐๐ก๐๐ซ
Wishing you a joyful, safe, and meaningful Independence Day!
God Bless America!
#July4th #IndependenceDay #RareDiseases #OrphanDrugs
Happy Canada Day! ๐จ๐ฆ
Wishing all our Canadian friends, customers, physicians and patients a joyful and proud celebration on this special national day.
#CanadaDay#Carthagenetics#RareDiseases
Wishing you a fantastic summer break! โ๏ธ
Weโre fully available in July for any questions about your orphan drug candidates and early access opportunities in Europe.
Feel free to contact us anytime.
[email protected] | +41 76 717 37 65
๐๐ฎ๐ฝ๐ฝ๐ ๐ฆ๐น๐ผ๐๐ฒ๐ป๐ถ๐ฎ ๐ฆ๐๐ฎ๐๐ฒ๐ต๐ผ๐ผ๐ฑ ๐๐ฎ๐! ๐ธ๐ฎ
Celebrating the proclamation of independence on June 25, 1991. Warm wishes to our Slovenian friends, physicians and patients.
#SloveniaStatehoodDay#DanDrzavnosti
๐๐ฎ๐ฝ๐ฝ๐ ๐ค๐๐ฒ๐ฏ๐ฒ๐ฐ ๐ก๐ฎ๐๐ถ๐ผ๐ป๐ฎ๐น ๐๐ฎ๐!
I am proud to have collaborated with talented Quebec partners, including Clementia Pharmaceuticals on Fibrodysplasia Ossificans Progressiva (FOP), Theratechnologies on Tesamorelin for Lipodystrophy, and with Quebec physicians on the very first gene therapy approved in Europe โ Glybera (alipogene tiparvovec) by uniQure for Lipoprotein Lipase Deficiency.
These partnerships reflect the excellence and forward-thinking approach that define Quebecโs biotech ecosystem.
Wishing all our Quebec friends, colleagues, and patients a joyful and proud Fรชte Nationale!
#FeteNationale #QuebecNationalDay #RareDiseases #OrphanDrugs #GeneTherapy
๐๐๐ฅ๐ฅ๐ฎ ๐๐๐๐ฃ๐ฉ ๐ ๐ค๐๐ฃโ๐จ ๐ฟ๐๐ฎ & ๐๐๐๐จ๐ช๐ข๐ข๐๐ง!
As bonfires light up the sky, we think of all children with rare diseases and their families. May this season of light bring you hope and strength.
#Midsummer#RareDiseases
Happy Festa della Repubblica! ๐ฎ๐น
Celebrating the birth of the Italian Republic in 1946. Grateful to Italy for pioneering early access through Laws 648 & 326, giving rare disease patients faster access to innovative treatments. #FestaDellaRepubblica#RareDiseases
Happy 1st of June! โ๏ธ
What a beautiful start to the summer season โ longer days, warmer light, and nature in full bloom.
To all students currently taking exams: we wish you calm, confidence, and great success!
May this month also be an invitation to enjoy precious moments with family and loved ones.
Wishing everyone a wonderful week ahead filled with energy and joy!
Happy Dan drลพavnosti! ๐ญ๐ท
Warm congratulations on Croatia Statehood Day. Thank you to Croatian physicians, health authorities and patient groups for their dedication to rare disease patients. #DanDrzavnosti#Carthagenetics#RareDiseases
Chers amis, chers collaborateurs, chers membres de ma famille musulmane,
En ce jour de fรชte, je vous souhaite de tout cลur un joyeux Aรฏd Mubarak ! Que cette cรฉlรฉbration vous apporte paix, joie, partage et de prรฉcieux moments avec vos proches. Que vos cลurs soient remplis de gratitude et dโamour.
En tant que vรฉgรฉtarien depuis de nombreuses annรฉes, je vis cette pรฉriode avec des sentiments partagรฉs. Je respecte profondรฉment votre foi et vos traditions, et je suis heureux de vous voir rรฉunis dans la joie et la gรฉnรฉrositรฉ. Cependant, je ne peux pas taire la souffrance inutile que reprรฉsente, ร mes yeux, le sacrifice des animaux. Chaque รชtre vivant ressent la peur et la douleur, et mon cลur se serre en pensant ร eux.
Je vous adresse ce message avec beaucoup de bienveillance et sans jugement : puissions-nous tous, chacun ร notre faรงon, chercher ร rรฉduire la souffrance autour de nous. Que cette Aรฏd soit aussi lโoccasion de rรฉflรฉchir ร la compassion que nous pouvons รฉtendre ร tous les รชtres.
Je vous embrasse trรจs fort et vous souhaite une belle fรชte, pleine de sens, de partage et de douceur.
Avec toute mon affection,
Proud to join todayโs FDA & Triangle CERSI workshop on Advancing Novel Surrogate Endpoints for Rare Disease Drug Development.
Strongly committed to faster, smarter pathways for patients.
#RareDiseases#OrphanDrugs#FDA
Today is International Day Against Homophobia, Transphobia and Biphobia (IDAHOT).
We stand firmly against all forms of discrimination and hatred based on sexual orientation or gender identity.
Every person deserves respect, dignity, and the right to live freely and safely. In our community and in healthcare, inclusion is not optional โ it is essential.
Letโs continue building a world where everyone feels seen, valued, and protected.
#InternationalNursesDay! Thank you to all nurses for your incredible dedication, especially those caring for rare disease patients on lifelong treatments. You are true heroes. ๐
#RareDiseases#OrphanDrugs