UF Powell Center

[UF Powell Center @ufpowellcenter]

@BarthSyndrome @US_FDA A powerful story of hope. Meet Abe!

[Laura Hagerty @Hagerty_Laura]

“The strength of evidence for both efficacy and safety of #vamorolone over such a wide dose range…allows clinicians to individually tailor treatment of #Duchenne patients” said Craig McDonald, MD, a professor at the University of California, Davis.

[UF Powell Center @ufpowellcenter]

https://t.co/pqqID6eZrV

[UF Powell Center @ufpowellcenter]

https://t.co/pqqID6eZrV

[ASGCT @ASGCTherapy]

"Mavis was not only a world class scientist, but her character and passion were also unparalleled." Read this tribute to Mavis Agbandje-McKenna, Ph.D. (@UF), the recipient of our 2020 Outstanding Achievement Award. https://t.co/CPZ76pjw8R

[UF Powell Center @ufpowellcenter]

Today is #RareDiseaseDay – so we want to recognize the 7,000 rare diseases that collectively affect more than 30 million people in the US and 300 million people worldwide. Today and every day we are committed to serving those living with #raredisease.

[Barry Byrne @barrybyrne1]

Provention Bio Announces Key Findings from Pre-clinical Proof-of-concept Study for PRV-3279 for the Prevention of ... https://t.co/FFYK7nSCYa

We are delighted to partner with ProventionBio to conduct this important study @ufpowellcenter

[UF Powell Center @ufpowellcenter]

@NIHDirector @JoeBiden Absolutely awesome !!!

[Sarepta Therapeutics @Sarepta]

Today we announced an investment in @AavantiBio, an exciting advancement in building our #genetherapy engine, to bring meaningful therapies to patients and families impacted by #raredisease. Learn more: https://t.co/9xEu1WZmcm

[Sarepta Therapeutics @Sarepta]

Today we announced a collaboration with @UF to enable cutting-edge research for novel #geneticmedicine, through the funding of multiple innovative research programs. Read our press release to learn more: https://t.co/4EMlnqRsRX SRPT

[UF Powell Center @ufpowellcenter]

Thanks to Jordan’s family for all you do! https://t.co/oafpZOT5Bg

[Duchenne UK @DuchenneUK]

Yesterday, we held a webinar to give updates on gene therapy and our new £500,000 grant to overcome gene therapy immunity challenges.

You can watch the recording here:
https://t.co/NMGSSiFJqa

[UF Powell Center @ufpowellcenter]

Solving the immune response in AAV gene therapy is especially important in DMD. Thanks @DuchenneUK !!!

[Duchenne UK @DuchenneUK]

We grant £500,000 to world leaders in #genetherapy & AAV immunology at the Powell Gene Therapy Center, University of Florida, to try to temporarily modify the immune system so that anybody can be treated with gene therapy and receive repeat doses:

https://t.co/r9ABnVzROE

[UF Powell Center @ufpowellcenter]

https://t.co/CJ31sr3hoN

[UF Powell Center @ufpowellcenter]

Denison Magazine - The Idea Guy - Barry Byrne ’78 has spent his career searching for cures to rare childhood diseases. His latest tool, gene therapy, is about to go mainstream—and change the way we heal. - https://t.co/TP6lt6DL4X

[UF Powell Center @ufpowellcenter]

https://t.co/o0aKdBhb9b

Harnessing the power of gene therapy against SARS-CoV2. Observing an immediate immune response with high level antibodies after a single dose of the vaccine.

[Dr. Sanjay Gupta @drsanjaygupta]

By now, you probably recognize the gravelly, calming voice of Dr. Anthony Fauci. For decades, he has been at the forefront of our public health crises. And, for the last 20 years, he has been a friend. Today’s podcast is essential, informative and personal
https://t.co/draK0GKXm4

[Hematopoiesis News @Hema_News]

Researchers report that up to 12-fold enhancement in the transduction efficiency of adeno-associated virus 6 vectors can be achieved in primary human #HematopoieticStemCells with polyvinyl alcohol. @ufpowellcenter https://t.co/eCldTFqZ1K

[Scott Gottlieb, MD 🇺🇸 @ScottGottliebMD]

Useful primer on the benefits of masks. A recommendation from CDC for consumers to wear cotton masks (with guidelines on how to fashion these products from household items) can improve safety and reduce spread and not strain the hospital supply chain. https://t.co/yAEi8hcLAH

[UF Powell Center @ufpowellcenter]

https://t.co/oPRIUrBCdr