ARDAT-Accelerating Research & Innovation for ATMPs
@AAtmps
The overall objective of ARDAT is to develop and provide the data and tools to fill gaps in our knowledge base in the areas of gene and cell therapies.
Coordinated by Dr. Martin Schulz of @pfizer & Prof. Mimoun Azzouz of @sheffielduni, ARDAT is a private-public partnership aiming to develop safer and more effective gene therapies for rare diseases. ARDAT is funded by @IHIEurope, @HorizonEU (grant agreement 945473) & @EFPIA.
Imlifidase, a new option to optimize the management of patients with hemophilia A on emicizumab - a paper by the Lacroix-Desmazes team has been published in JTH: https://t.co/XjcpDh7qR4! Thx 2 @IHIEurope, @HorizonEU, @AgenceRecherche, @BayerPharma, @spark_tx 4 the funding!
⏰Applying for IHI call 3? The deadline is one month today!
👉 Get the details on the topics: https://t.co/2eY7Hktf8b
👉 Catch up on the Call Days: https://t.co/YrSRwFKExf
❓ Got questions? Contact us: https://t.co/w9EGNPKro0
Good luck! 🍀🍀🍀
#HorizonEU#EUHealthResearch
The ceremony also raises money for #RareDiseaseDay!
Why not join us in celebrating our incredible awardees and their phenomenal achievements, while also raising money for those people and organisations doing amazing things?
Register👉 https://t.co/jjuFdBj95X
#EURORDISAwards2023
UK ATMP #ClinicalTrials Report 2022:
- The UK’s portfolio of ATMP clinical trials continues to grow
- Oncology remains the largest therapeutic area
- Majority of therapies in the database are genetically modified
https://t.co/WDQY6VfeR5
#ClinicalTrials
Mimetas is a valued member of the IHI Funded ARDAT Consortium which seeking to provide tools to accelerate the development of advanced therapies https://t.co/kMKoyVDwcq @IHIEurope
Get ready to #GrowLearnDiscover this Thursday from our stunning studio location! 📸 Prepare to immerse yourself in a world of all things human tissue models at our 10-year anniversary event.
Full program: https://t.co/jbrXRIVFXg
Register here: https://t.co/PCdbefqA9p
[On recrute] @GenethonFr leader de la #TherapieGenique pour les maladies rares, est à la recherche d’un Ingénieur Développement au sein du service CMC Analytique.
Postulez dès maintenant !
👉🏼https://t.co/doLxBYWWty
#AAV is popular in #genetherapy, but has affinity for the liver—unhelpful If affected cell type is located in another organ. ASGCT members Francesco Puzzo @cicciopuz & Mark Kay engineered AAV vectors that increased transduction of #cancer cell lines #MTNA https://t.co/MVpq5FBgo9
Did you know that the Gene Therapy Innovation and Manufacturing Centre (GTIMC), which has close ties with ARDAT will tackle the major challenges in gene therapy development for some of the most devastating rare diseases. https://t.co/4tVsuRlbje
Monday is the kickoff for #RareDiseaseWeek in #Brussels! EveryLife will be there to show our continued support @Eurordis and 44 patient advocates from 21 countries who are sharing their rare disease journeys with #EU lawmakers. Many languages, one #raredisease voice!
Find out more about the ARDAT project led @neuroshef who with 34 partners across 10 countries aims to accelerate cell and gene therapies #SITraN @sheffunimdh @sheffielduni
Listen to ASGCT's Giants of #GeneTherapy#Podcast! Society President @HPKiem, MD, PhD, regularly interviews luminaries in the worlds of cell & gene therapy. Episodes with David Baltimore, PhD; Kathy High, MD; Carl June, MD @carlhjune, are out now: https://t.co/yj7fQgONEQ
A team from @NorthwesternU has created the 1st highly mature #neurons from human #iPSCs using a synthetic material, opening up new opportunities for mechanism research and therapy development for neurodegenerative diseases and traumatic injuries.
Read now: https://t.co/wfZIeT2Cfr
We've launched a survey with @Access4Labs for lab scientists who are disabled/living with chronic health conditions. Your feedback can help us to study and improve access issues.
Complete the survey: https://t.co/wgUAp5iUsC
#AccessAllAreasLab#HealthBiotech
Late breaking news: first publication of the ARDAT Consortium: "Current global regulatory landscape for biodistribution & shedding assessment of rAAV gene therapies & recommendations of the IMI ARDAT consortium on future directions". Congratulations to the WP5 Team.
Recombinant AAV (#rAAV) is used to deliver therapeutic genes to treat #rarediseases. This study from #MTMCD on rAAV production could inspire design of next-generation manufacturing platforms to support safe, effective, and affordable AAV-based #genetherapy https://t.co/oGmwxLLvHT