In a major milestone for science, for medicine, and for patients, the world’s first CRISPR drug has been approved in the UK.
“A new treatment for sickle-cell disease and transfusion-dependent β-thalassemia has been authorised by the Medicines and Healthcare products Regulatory Agency (MHRA) for patients aged 12 and over after a rigorous assessment of its safety, quality and effectiveness.”
Congratulations to the many scientists, doctors, patients, and industry leaders who made this development possible.🍻
https://t.co/pUL956YsG3
It’s a platform presentation sweep for the @WangLysolab!
Seven submitted abstracts, seven platform presentations at the 2024 @WORLDSymposia !
San Diego here we come!
Congrats to Jerry Harb, who persevered through the project (his 1st with our lab) and paper writing (our lab’s 1st/not last #CRISPR therapy paper)!
Team effort from all including @CLChristensen23, Alli, and Perla (OTEs), @kansh0524 (sequencing), and @GreenwoodGenCtr (FSA)
Gene editing landscape
I pulled together 42 public & private companies and charted the preclinical & clinical assets of each, segmented by approach & editor
Some takeaways:
One of our fantastic Research Scientists, @CLChristensen23, then published her work in generation and characterization of two human Pompe disease fibroblast-derived iPSC lines.
https://t.co/unlPNKHikc
Here’s my offer. I will give you 100% of your rent up to $2000 if you help me spread the #staythefuckhome message by retweeting this, following me, and tagging someone that is #stayingthefuckhome.
EXCITING NEWS! Registration now open for our 4th ANNUAL MAY SYMPOSIUM! Featuring Dr. Harry Atkins, Dr. Jeff Biernaski, Dr. Ly Vu, Dr. Massimiliano Paganelli and MORE! Register here: https://t.co/fX5PRWXObD !
Shout out to the amazing @WomeninSciUVic team for putting on another successful #STEMSymposium on Nov 28th! This team is incredible. Thanks to everyone who presented, volunteered and attended!
📷Emma Wells-Durand
Welcome to read this paper "Cell and Gene Therapies for Mucopolysaccharidoses: Base Editing and Therapeutic Delivery to the CNS" by Dr. Francis Y. M. Choy
https://t.co/lJFpvF040f
Wow - what an inspiring talk from an incredible young woman in STEM! 18 yo Ella Chan describes the importance of mentorship @CC_STEM @WomeninSciUVic #yyj@UBCWomenInSCI
“A leader needs to show vulnerability...” discussing non-threatening environments to succeed, fail, and grow @CC_STEM Innovation driven by diversity panel @annastukas@AlisonVAnderson
Fabulous morning keynote @CC_STEM 6.0 by @MicheleRomanow One of many key takeaways: a universal precursor in any field is “how often you have to fail to be successful.”
Excited to attend SFU WWEST Creating Connections 6.0 conference May 3rd & 4th @ DT Vancouver. Looking forward to participating in meaningful dialogue on diversity in STEM fields. @CC_STEM https://t.co/yyxSo0fmBJ