DeFi

#Duchenne #Elevidys

[Rare Diseases @CheckOrphan]

Avidity Biosciences’ Del-zota Demonstrated Reversal of Disease Progression Across Key Functional Endpoints in Phase 1/2 Trial for People Living with DMD44 - For More Information Visit https://t.co/F35Bz1hugu @aviditybio #DMD #Duchenne #DMD44 #Rare_Diseases #OrphanDrugs

[Muscular Dystrophy News Today @mdnewstoday_]

Agamree, an approved steroid treatment for Duchenne MD, will be sold in Turkey by GEN, per an agreement with Santhera. https://t.co/6WgPH5IJwm

#musculardystrophynews #musculardystrophy #musculardystrophycommunity #livingwithMD

[GENETHON France @GenethonFr]

🚀 @GenethonFr lance la phase pivot de son essai de thérapie génique GNT0004 pour la myopathie de Duchenne !
✅Autorisations 🇫🇷 ANSM (EMA) & 🇬🇧MHRA
✅ 64 enfants inclus
✅ Dose efficace : 3x10¹³ vg/kg
📅Inclusions dès août/septembre
https://t.co/ZZ1qAVXW68
#Duchenne

[Legitimate Targets @LegitTargets]

🚨🇧🇷🇿🇦 BREAKING: BRAZIL to formally join South Africa's GENOCIDE LAWSUIT against ISRAEL at the International Court of Justice.

[DMD Companion @DMDCompanion]

New article posted on DMD Companion: "New genetic therapy shows promise in improving muscle health in DMD." Read the full article here: https://t.co/YgL0O9nasj #DMD #Duchenne

[DMD Dayanışma Platformu @DMDdayanisma]

#Elevidys Avrupa İlaç Ajansı'ndan Onay Alacak mı? #EMA Onayı Türkiye'deki #DMD Hastaları İçin Ne Anlama Gelecek?

#DMDdayanışma #Duchenne

https://t.co/WdOyWqUxUh

[Parent Project Muscular Dystrophy (PPMD) @ParentProjectMD]

Today @Sarepta announced positive topline results from Part 2 of EMBARK, the company’s Phase 3 clinical study of ELEVIDYS for individuals living with #Duchenne. Learn more: https://t.co/qeURG1xoeF

[MrBeast @MrBeast]

Just uploaded a video where we helped 2,000 amputees walk again. Many lived in America and it feels so disgusting that in a country with this much wealth, a fucken YouTuber is their only option to get a prosthetic leg. We need to fix this.

[DMD Warrior @dmdwarriorcom]

Plans for DYNE-101 in DM1 and DYNE-251 in DMD Are Announced by Dyne Therapeutics

👉 Read More: https://t.co/6jwGJqdCfM

#dmd #duchenne #bmd #becker #genetherapy #dmdwarrior #dmdwarriors #duchennesmusculardystrophy #musculardystrophy #gene #dna #dyne #dyne251 #dyne101

[CureDuchenne @CureDuchenne]

Dyne plans to submit for FDA Accelerated Approval for Duchenne exon 51 skipping in 2026; Trial still recruiting participants. #exonskipping #DMD #Duchenne #CureDuchenne #Dyne #musculardystrophy #FDA https://t.co/POzyiSOeU0

[DeFi @Decentr_DeFi]

@KashPatelX Yes

[Lucid @LucidCiC]

$ADA is going to Double Digits!📯

Cardano will Conquer the Top 3 during its Parabolic Rise in 2025 because it is the only Chain capable of securing the Trillions of Dollars in assets flowing across the Globe!

Whether you Like it or Not, Cardano will Flip Everything!

$ADA 👑

[DeFi @Decentr_DeFi]

@DMDTurkiye all children should live. our children will be better than us

[DMD Türkiye @DMDTurkiye]

🇹🇷DMD Türkiye olarak çocuklarımızın sesini her platformda duyurmaya devam ediyoruz!

Bu kez ulusal haber kanallarından tüm Türkiye'ye bir kez daha sesleniyoruz:
"DMD çaresiz değil, çare sizsiniz!

Çocuklarımızı ancak bilim ve toplumsal farkındalık kurtarabilir. Yurt dışında onaylanan ilaçların ülkemizde de karşılanması, DMD'nin kaderini tamamen değiştirecek. 7500 DMD hastası evladımızın sizden tek isteği var: Yanlarında olun ve sessiz çığlıklarını duyun.

Hadi, gelin birlikte bu yükü hafifletelim. Düşenin dostu olun, DMD bitsin!
Eğer daha fazlasını yapamıyorsanız bile, sadece bu gönderiyi paylaşarak bile fark yaratabilirsiniz. Çünkü birlikte daha güçlüyüz! #7500AileİlaçBekliyor @cnnturk

[Muscular Dystrophy Association @MDAorg]

#Duchenne #MuscularDystrophy is a rare genetic disorder caused by mutations in the dystrophin gene that lead to loss of the dystrophin protein. Learn more about the symptoms, causes, and current therapies available: https://t.co/klSwiN16kO