SMA Research

Spinal Muscular Atrophy scientific research news from around the world. Follow @smatrust for general SMA Trust information and fundraising updates.

[SMA Research @SMAresearch]

Today is #UKSMAAwarenessDay! Spinal Muscular Atrophy is a rare, genetically inherited neuromuscular condition. Please retweet to help raise awareness of #SMA

[SMA Research @SMAresearch]

UK #SMA Research conference attendees, representing @NDCNOxford @EdinUniNeuro @neuroshef SMAReach @UCL_ICH @ryanezmunoz @ISTM_Keele @univofstandrews - Mostly all funded by @smatrust at some point!

[SMA Research @SMAresearch]

A day at #SITRAN, finding out what the UK #SMA laboratories are working on. Keynote delivered by Prof Azzouz on DNA damage in SMA.

[SMA Research @SMAresearch]

End-of-study results from Biogen's CHERISH trial demonstrate stabilisation or improvement in motor function in individuals with #SMA, where the natural history of the disease is a decline in motor function over time.
https://t.co/MW2g6OLrUU

[SMA Research @SMAresearch]

#SMAEurope held its first international scientific congress on #SMA in Krakow, Poland 🎓. It was a huge success. Find out more from @drgroen : https://t.co/SJLcuEctb3

[SMA Research @SMAresearch]

Scottish Medicines Consortium will be assessing #nusinersen for patients with SMA. We will be working with @SMASupportUK & @smatrust to provide a Patient Group Submission. #SMA

[SMA Research @SMAresearch]

RT @amrc: Please read our statement on the Government's announcement of a new accelerated access pathway: https://t.co/f9kgclAXF2 #sma

[SMA Research @SMAresearch]

RT @SMAEurope: 2 days left before abstract submisson deadline 4 our int. scientific Congress on #SMA. Get them in! https://t.co/3gGFEUvuyK

[SMA Research @SMAresearch]

Roche provided a community statement on the SUNFISH clinical trial RG7916 for #SMA. Find out what it says here: https://t.co/zGpbIVDYll

[SMA Research @SMAresearch]

Can you help? https://t.co/X5jPO2bOA1

[Brunhilde Wirth @BrunhildeWirth]

We expect an exiting meeting with top invited speakers, oral presentations from selected abstracts, posters, workshops, prizes. Do not miss! https://t.co/Tim0828niJ

[SMA Research @SMAresearch]

AveXis 2 initiate pivotal trial for gene replacement product, AVXS-101, in #SMA Type 1 in the U.S. https://t.co/LilvKyFuNf

[SMA Research @SMAresearch]

Roche announces start of the 2nd part of the Phase 2 #SUNFISH clinical trials 4 Type 2/3 #SMA. Find out more: https://t.co/U7TiCASPFk

[SMA Research @SMAresearch]

NHS England to fund hospital costs of administering #Spinraza 4 patients with #SMA Type 1 on Biogen’s EAP. https://t.co/KBnsWrEUsc

[SMA Research @SMAresearch]

SRK-015, a potential new #SMA therapy by Scholar Rock, 2 enter clinical trials soon, based on encouraging data: https://t.co/PX6hIEWpw0

[SMA Research @SMAresearch]

Biogen provides a summary of discussion between @SMAEurope & Biogen reps on EU list price for #nusinersen. #sma https://t.co/NS4zqmBtbB

[SMA Research @SMAresearch]

All Party Parliamentary Group to discuss access to #nusinersen in the UK at the Houses of Parliament #sma #spinraza: https://t.co/b98mmCPFdo

[SMA Research @SMAresearch]

Read our update from an NHS England meeting on the SMA Type 1 Expanded Access Programme 4 #nusinersen #spinraza #sma https://t.co/niEP9PCnFu

[SMA Research @SMAresearch]

New #SMA research grants awarded by @SMAEurope following recommendations by its Scientific Advisory Board. Find out: https://t.co/1NJTD9hWuV