Help4HD

Help4HD-International, is a non profit organization serving the #Huntingtonsdisease and #JuvenileHuntingtonsdisease community.

[Help4HD @Help4HDI]

Breaking News: The FDA Approves the BLA Submission for AMT-130 through the FDA Accelerated Approval Pathway
A statement from our CEO, Katie Jackson: “Today marks a turning point in medical history for HD in the United States, as the approval of the BLA submission through the accelerated approval pathway for AMT-130 for Huntington’s disease transforms hope into tangible progress—proving that urgency and innovation can rewrite the future for patients and families. I have had the honor of working on projects with the FDA since 2014. The one thing I have learned over the years is that the partnership between the FDA, the trial sponsors, and the HD community is the only one that will help expedite drug development and get products over the finish line. I am so thankful to the clinical trial participants more than anyone else for making the brave decision to participate in a clinical trial, to the 51,000 people who signed the petitions, uniQure for fighting through, and the FDA that listened to us and utilized regulatory flexibility through one of their promising pathways to get this to the next step. We are truly grateful. Today is a historic day, and I am so thankful to uniQure and the FDA for allowing me to be a part of it. This milestone proves that when science and determination unite, we can bring light to even the darkest of battles and offer new possibilities for generations to come.”
https://t.co/72V9UfLPrc

[Help4HD @Help4HDI]

A huge thank you to @knotts Berry Farms for offering free admission tickets to the theme park. Excited to see pictures of all #HD families going to the park to spend time with their families & community before #Help4HDHIPE2026, #LosAngelesCA on July 18!

[Help4HD @Help4HDI]

A huge congratulations to Prilenia and Ferrer on this very exciting news! Prilenia and Ferrer Announce Initiation of the Confirmatory PRECISE-HD Study of Pridopidine in #HuntingtonsDisease. #Help4HD #HDResearch #Blog

https://t.co/TSgfESHNKZ

[Help4HD @Help4HDI]

We want to invite you to this special social hour for #AtRisk/#GenePositive members of the #HD Community & the individuals supporting them on their HD journey!

Tuesday Talk Time
Tuesday 4-5PM PST
Connect with people that "get it"
Details: [email protected]

[Help4HD @Help4HDI]

Proposed change to how federal grants — incl. #HDResearch funding — are awarded & managed incl. political appointees, not scientists, could get final say over which research gets funded. Warned rule could politicize American science.

https://t.co/CBcCpXt9eh

[Help4HD @Help4HDI]

MONDAY MIXER! Connect tomorrow at 4pm PST on Zoom to hang out with our HD community at this relaxed social. Reach out to [email protected] for more details. See you soon!

[Help4HD @Help4HDI]

Hear from Dr. Emily Lefler, Novartis Clinical Development Medical Director, to learn more about INVEST-HD focusing on Votoplam. Current #HDResearch & more at this #FREE #HD #Education event on July 18! #Help4HDHIPE2026 #LosAngelesCA

https://t.co/oF1oE5X9sv

[Help4HD @Help4HDI]

Introducing DJ & Bill! These gentlemen will be presenting Help4HD's NEW Men's Meet Up at Los Angeles HIPE! #Register below to meet us there or listen via LIVE stream on Facebook! #Help4HDHIPE2026 #LosAngelesCA #HuntingtonsDisease

https://t.co/oF1oE5XHi3

[Help4HD @Help4HDI]

This guide provides practical techniques & strategies designed to enhance independence & reduce injury risk for people with disabilities..." ~ Getting In & Out of a Car Guide💙💜💙

#Help4HD #Resource Database: https://t.co/LOi2DDujDT

[Help4HD @Help4HDI]

"When I found out my sister and I had a 50/50 chance I was even more petrified..." Hear how #HD came into Ilana & her sister's life via internet search on #Help4HDTV & how they faced this news during their college years. #GeneticTesting #FamilyDisease

https://t.co/gVpIdASXcQ

[Help4HD @Help4HDI]

Tomorrow’s video features Ilana Rubin talking about testing same time as her sister with differing results. Listen on #Help4HDTV! #HuntingtonsDisease #genetictesting

https://t.co/PW3s37HD4q

[Help4HD @Help4HDI]

Thank you for supporting #HIPE! We are so grateful to our #sponsors that make these events possible so we can deliver credible education, information, & resources to our #HD community! #Help4HDHIPE2026 #LosAngelesCA

Event details: https://t.co/oF1oE5XHi3

[Help4HD @Help4HDI]

Find details on the Huntington's Post about the real-world data presented at the HDSA Conference 2026! #HuntingtonsDisease #Chorea #HDSymptom

Read more: https://t.co/4QwOP5qC0N

[Help4HD @Help4HDI]

#LEEP's next educational endeavour is coming up this summer! We are excited to be exhibiting at the Crisis Intervention Team International Conference & continue raising awareness for #HuntingtonsDisease! #Help4HD #LawEnforcement #HDAwareness

[Help4HD @Help4HDI]

Monday Mixer! Check your time zone & see if you can make this casual social with #HD community members on Zoom! Reach out to [email protected] for more details. #Help4HD #MondayMixer #HuntingtonsDisease

[Help4HD @Help4HDI]

Meet the #HDExperts on out HIPE panel ready to answer your questions at our Help 4 HD event! #Help4HDHIPE2026 #LosAngelesCA #HuntingtonsDisease

🔹 Dr. Sasha Duffy
🔹Susan Reynolds
🔹 Lisa Mooney
🔹 Dr. Adys Mendizaba

Register here: https://t.co/oF1oE5XHi3

[Help4HD @Help4HDI]

"...outdoor learning experience for children & adults with special needs. This barrier-free camp welcomes people of all ages & #disabilities...Great Lakes Bay Region in #Michigan." ~Camp Fish Tales💙💜💙

#Help4HD #Resource Database: https://t.co/yPkqCPSbqS

[Help4HD @Help4HDI]

What does having children look like after participating in #HD #GeneTherapy? Listen to answers to this question & more on #Help4HDTV! #HuntingtonsDisease #HDResearch

https://t.co/PW3s37HD4q

[Help4HD @Help4HDI]

Learn more about therapies, social security, & more on this week's episode of #Help4HDTV! Tune in TOMORROW at 9am PST! #HuntingtonsDisease #HDResearch #UnmaskingTheTruth

https://t.co/PW3s37HD4q

[Help4HD @Help4HDI]

We want to thank our Support Group #Sponsors! We couldn’t do what we do without partners like you. Thank you for helping us remind individuals impacted by #HD that they are not alone. #Help4HD #SupportGroup

Find support: https://t.co/G6VZXwk9BX

[Help4HD @Help4HDI]

It's time for Monday Mixer! Join us this week on Zoom at 4pm PST for fellowship with #HD community members at this weekly social! Reach out to [email protected] for more details. See you soon!