@Bios_n_Techs@avidresearch Maybe muscle deterioration is irreparably high at higher ages. DMD patients can be in a wheelchair when 10 years old. Wonder what outcomes would have been with a study in babies like AVXS-101 did
@portefeuillefun@AAMortazavi That would only happen when Aat van Herk pushes for an aggressive exitstrategy and Onno retires. And Onnos dream is to create drugs for patients and I think he doesnt feel so good about filgo anymore