#Breaking: The European Commission approves CRISPR/Cas9 gene-edited treatment, co-developed with Vertex Pharmaceuticals, for #SickleCellDisease and #BetaThalassemia for the European Union. Learn more: https://t.co/94JrUPfhMT
Register for this *FREE* virtual symposium with a stellar lineup of pioneering speakers!
Come learn about the challenges & progress in the gene editing field!!
🧬🔧🎖️
@lab_davidson@skathire@davidrliu & many others!
ASTONISHING+EXHILARATING:
31 patients with SCD free of pain post-CRISPR-gene-editing!
42/44 with thal are transfusion-free!!
AND approach being advanced to to the pediatric population!!!
Bravo, @CRISPRTX CMC team.
♥️ 👏 Stu Orkin + @danielevanbauer
https://t.co/r7DSlwjQXJ
We are pleased to announce new clinical data on our investigational gene-edited therapy for the treatment of sickle cell disease and beta thalassemia at the @EHA_Hematology 2022 Congress. Learn more: https://t.co/AUpiyc1vQB #EHA2022
We’re pleased to share that an abstract on safety and efficacy data from the ongoing CTX130™ clinical trial for patients with T-cell lymphoma has been accepted for an oral presentation at the @EHA_Hematology 2022 Congress. Learn more: https://t.co/IaQYijzwNZ #EHA2022
Today we report in @CellCellPress an engineered virus-like particle (eVLP) platform that mediates efficient in vivo delivery of therapeutic proteins, including base editors and Cas9 nuclease, resulting in therapeutic editing in multiple mouse organs. 1/14
https://t.co/v1yBl296L6
Wow.
“4 genes were knocked out…including one that encodes a molecule that causes an aggressive human rejection response.
A growth gene was also inactivated to prevent the pig’s heart from continuing to grow…6 human genes were inserted…to make the porcine organs more tolerable”
Therapeutic mRNA for heart failure?!
Our own Joel Rurik (@DevBioAcademic) teamed up with @WeissmanLab to make CAR T cells entirely in the body to treat heart disease.
Published today on the cover of Science!
https://t.co/f3UZrNikNs
@CAMBUpenn@PennBGS@ScienceMagazine
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🔊In a few days, we head to the printers' to print the first batch of orders. If you want to be among the first receivers of the new #LabhoppingCalendar this month, then don't wait. Book your copy at 15% discount & free shipping now! Link: https://t.co/9RO6WEcsY1
We are pleased to announce that the U.S. FDA has granted Regenerative Medicine Advanced Therapy (RMAT) designation to CTX110™ for the treatment of relapsed or refractory CD19+ B-cell malignancies. Learn more here: https://t.co/P6b6IUDcEO