A milestone in modern medicine: 1st therapeutic in vivo gene editing in human patients!
From Julian Gillmore, @intelliatweets & colleagues out today @NEJM:
https://t.co/4xyyFHAwAj
Here’s an overview of a new potential treatment for transthyretin (ATTR) amyloidosis.
(thread)
Great start to #AABB20. Looking forward to the Plenary session tomorrow night followed by Q&A! I will talking about the novel role of L-plastin in platelet production. Thank you #AABB20 for this opportunity to present my research and humble to receive outstanding abstract award.
New 3i Investigator Article Alert!! miR-125a-5p Regulates Megakaryocyte Proplatelet Formation Via the Actin Bundling Protein L-Plastin. https://t.co/MKjQNPc8qq #sciencetwitter#academictwitter#researchmatters
A really intriguing study on ex vivo gene editing of HSCs!
Ex vivo editing of human hematopoietic stem cells for erythroid expression of therapeutic proteins | Nature Communications https://t.co/P4gHmQRi12